From the Laboratory of Persistent Viral Diseases, Rocky Mountain Laboratories, NIAID, National Institutes of Health, Hamilton, Montana 59840.
J Biol Chem. 2014 May 2;289(18):12245-63. doi: 10.1074/jbc.M114.556639. Epub 2014 Mar 13.
In prion-infected hosts, PrPSc usually accumulates as non-fibrillar, membrane-bound aggregates. Glycosylphosphatidylinositol (GPI) anchor-directed membrane association appears to be an important factor controlling the biophysical properties of PrPSc aggregates. To determine whether GPI anchoring can similarly modulate the assembly of other amyloid-forming proteins, neuronal cell lines were generated that expressed a GPI-anchored form of a model amyloidogenic protein, the NM domain of the yeast prion protein Sup35 (Sup35(GPI)). We recently reported that GPI anchoring facilitated the induction of Sup35(GPI) prions in this system. Here, we report the ultrastructural characterization of self-propagating Sup35(GPI) aggregates of either spontaneous or induced origin. Like membrane-bound PrPSc, Sup35(GPI) aggregates resisted release from cells treated with phosphatidylinositol-specific phospholipase C. Sup35(GPI) aggregates of spontaneous origin were detergent-insoluble, protease-resistant, and self-propagating, in a manner similar to that reported for recombinant Sup35NM amyloid fibrils and induced Sup35(GPI) aggregates. However, GPI-anchored Sup35 aggregates were not stained with amyloid-binding dyes, such as Thioflavin T. This was consistent with ultrastructural analyses, which showed that the aggregates corresponded to dense cell surface accumulations of membrane vesicle-like structures and were not fibrillar. Together, these results showed that GPI anchoring directs the assembly of Sup35NM into non-fibrillar, membrane-bound aggregates that resemble PrPSc, raising the possibility that GPI anchor-dependent modulation of protein aggregation might occur with other amyloidogenic proteins. This may contribute to differences in pathogenesis and pathology between prion diseases, which uniquely involve aggregation of a GPI-anchored protein, versus other protein misfolding diseases.
在朊病毒感染的宿主中,PrPSc 通常积累为非纤维状的、膜结合的聚集体。糖基磷脂酰肌醇 (GPI) 锚定的膜结合似乎是控制 PrPSc 聚集体生物物理性质的一个重要因素。为了确定 GPI 锚定是否可以类似地调节其他淀粉样形成蛋白的组装,生成了表达模型淀粉样蛋白的 GPI 锚定形式的神经元细胞系,即酵母朊病毒蛋白 Sup35 的 NM 结构域 (Sup35(GPI))。我们最近报道,在该系统中,GPI 锚定促进了 Sup35(GPI) 朊病毒的诱导。在这里,我们报告了自发或诱导起源的自我传播 Sup35(GPI) 聚集体的超微结构特征。与膜结合的 PrPSc 一样,用磷脂酰肌醇特异性磷脂酶 C 处理的细胞中,Sup35(GPI) 聚集体不易释放。自发起源的 Sup35(GPI) 聚集体是去污剂不溶性的、蛋白酶抗性的、自我传播的,这与报道的重组 Sup35NM 淀粉样纤维和诱导的 Sup35(GPI) 聚集体相似。然而,GPI 锚定的 Sup35 聚集体不能被淀粉样蛋白结合染料(如硫黄素 T)染色。这与超微结构分析一致,该分析表明聚集体对应于致密的细胞膜表面囊泡样结构的积累,而不是纤维状的。总之,这些结果表明,GPI 锚定指导 Sup35NM 组装成类似于 PrPSc 的非纤维状的、膜结合的聚集体,这增加了 GPI 锚定依赖性蛋白聚集可能发生在其他淀粉样蛋白的可能性。这可能导致朊病毒病(其独特之处在于 GPI 锚定蛋白的聚集)与其他蛋白质错误折叠疾病之间在发病机制和病理学上存在差异。