原发性免疫缺陷的造血干细胞移植
Hematopoietic stem cell transplantation for primary immunodeficiencies.
作者信息
Kang Elizabeth, Gennery Andrew
机构信息
Hematotherapeutics Unit, Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases, National Institutes of Health, 10-CRC Room 6-3752, 10 Centre Drive, Bethesda, MD 20892, USA.
Paediatric Immunology Department, Institute of Cellular Medicine, Great North Children's Hospital, c/o Ward 3, Queen Victoria Road, Newcastle upon Tyne NE1 4LP, UK.
出版信息
Hematol Oncol Clin North Am. 2014 Dec;28(6):1157-70. doi: 10.1016/j.hoc.2014.08.006. Epub 2014 Sep 16.
Abstract
Allogeneic hematopoietic stem cell transplantation has been shown to be curative for well-described as well as newly discovered immunodeficiencies. However, it is difficulty to define a universal transplant regimen given the rarity of these disorders and the varied pathophysiology these disorders encompass. This article discusses those primary immunodeficiencies most commonly treated by hematopoietic stem cell transplant and describes the transplant issues specific to these disorders.
摘要
同种异体造血干细胞移植已被证明对已明确描述的以及新发现的免疫缺陷具有治愈作用。然而，鉴于这些疾病的罕见性以及它们所包含的不同病理生理学特征，很难确定一种通用的移植方案。本文讨论了那些最常通过造血干细胞移植治疗的原发性免疫缺陷，并描述了这些疾病特有的移植问题。
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