Heuzé Yann, Holmes Gregory, Peter Inga, Richtsmeier Joan T, Jabs Ethylin Wang
Department of Anthropology, The Pennsylvania State University, 409 Carpenter Building, University Park, PA 16802, USA
Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, One Gustave L. Levy Place, Box 1497, New York, NY 10029-6574, USA.
Curr Genet Med Rep. 2014 Sep 1;2(3):135-145. doi: 10.1007/s40142-014-0042-x.
Craniosynostosis, a condition that includes the premature fusion of one or multiple cranial sutures, is a relatively common birth defect in humans and the second most common craniofacial anomaly after orofacial clefts. There is a significant clinical variation among different sutural synostoses as well as significant variation within any given single-suture synostosis. Craniosynostosis can be isolated (i.e., nonsyndromic) or occurs as part of a genetic syndrome (e.g., Crouzon, Pfeiffer, Apert, Muenke, and Saethre-Chotzen syndromes). Approximately 85 % of all cases of craniosynostosis are nonsyndromic. Several recent genomic discoveries are elucidating the genetic basis for nonsyndromic cases and implicate the newly identified genes in signaling pathways previously found in syndromic craniosynostosis. Published epidemiologic and phenotypic studies clearly demonstrate that nonsyndromic craniosynostosis is a complex and heterogeneous condition supporting a strong genetic component accompanied by environmental factors that contribute to the pathogenetic network of this birth defect. Large population, rather than single-clinic or hospital-based studies is required with phenotypically homogeneous subsets of patients to further understand the complex genetic, maternal, environmental, and stochastic factors contributing to nonsyndromic craniosynostosis. Learning about these variables is a key in formulating the basis of multidisciplinary and lifelong care for patients with these conditions.
颅缝早闭是一种包括一条或多条颅缝过早融合的病症,是人类相对常见的出生缺陷,也是仅次于唇腭裂的第二常见颅面畸形。不同的缝性颅缝早闭之间存在显著的临床差异,并且在任何给定的单缝颅缝早闭中也存在显著差异。颅缝早闭可以是孤立性的(即非综合征性的),或者作为遗传综合征的一部分出现(例如,克鲁宗综合征、 Pfeiffer综合征、Apert综合征、Muenke综合征和赛特勒-乔岑综合征)。所有颅缝早闭病例中约85%是非综合征性的。最近的几项基因组发现正在阐明非综合征性病例的遗传基础,并将新发现的基因牵涉到先前在综合征性颅缝早闭中发现的信号通路中。已发表的流行病学和表型研究清楚地表明,非综合征性颅缝早闭是一种复杂且异质性的病症,支持其有强大的遗传成分,同时伴有有助于这种出生缺陷发病机制网络的环境因素。需要进行大规模人群研究,而非基于单一诊所或医院的研究,研究对象为表型同质的患者亚组,以进一步了解导致非综合征性颅缝早闭的复杂遗传、母体、环境和随机因素。了解这些变量是为患有这些病症的患者制定多学科和终身护理基础的关键。