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Spot light on skeletal muscles: optogenetic stimulation to understand and restore skeletal muscle function.
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本文引用的文献

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Functional disruption of the dystrophin gene in rhesus monkey using CRISPR/Cas9.
Hum Mol Genet. 2015 Jul 1;24(13):3764-74. doi: 10.1093/hmg/ddv120. Epub 2015 Apr 9.
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AAV-8 is more efficient than AAV-9 in transducing neonatal dog heart.
Hum Gene Ther Methods. 2015 Apr;26(2):54-61. doi: 10.1089/hgtb.2014.128. Epub 2015 Apr 1.
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Off-target-free gene delivery by affinity-purified receptor-targeted viral vectors.
Nat Commun. 2015 Feb 10;6:6246. doi: 10.1038/ncomms7246.
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Adeno-associated viral (AAV) vectors do not efficiently target muscle satellite cells.
Mol Ther Methods Clin Dev. 2014;1:14038-. doi: 10.1038/mtm.2014.38.
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Precise correction of the dystrophin gene in duchenne muscular dystrophy patient induced pluripotent stem cells by TALEN and CRISPR-Cas9.
Stem Cell Reports. 2015 Jan 13;4(1):143-154. doi: 10.1016/j.stemcr.2014.10.013. Epub 2014 Nov 26.
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A phase 1/2a follistatin gene therapy trial for becker muscular dystrophy.
Mol Ther. 2015 Jan;23(1):192-201. doi: 10.1038/mt.2014.200. Epub 2014 Oct 17.

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