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Moving toward a gene therapy for Huntington's disease.

作者信息

Glorioso J C, Cohen J B, Carlisle D L, Munoz-Sanjuan I, Friedlander R M

机构信息

Department of Microbiology and Molecular Genetics, The University of Pittsburgh School of Medicine, Pittsburgh, PA, USA.

Department of Neurological Surgery, The University of Pittsburgh School of Medicine, Pittsburgh, PA, USA.

出版信息

Gene Ther. 2015 Dec;22(12):931-3. doi: 10.1038/gt.2015.102.

DOI:10.1038/gt.2015.102
PMID:26633828
Abstract
摘要

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Proc Natl Acad Sci U S A. 2015 Mar 31;112(13):E1632-41. doi: 10.1073/pnas.1423556112. Epub 2015 Mar 16.
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J Mov Disord. 2022 Jan;15(1):15-20. doi: 10.14802/jmd.21006. Epub 2021 Nov 17.
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Front Genome Ed. 2021 Feb 1;3:623519. doi: 10.3389/fgeed.2021.623519. eCollection 2021.
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Health Secur. 2017 May/Jun;15(3):296-302. doi: 10.1089/hs.2016.0120. Epub 2017 Jun 2.
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