《孤儿药法案》的目的是什么？
What Is the Purpose of the Orphan Drug Act?
作者信息
Herder Matthew
机构信息
Health Law Institute, Faculties of Medicine and Law, Dalhousie University, Halifax, Nova Scotia, Canada.
出版信息
PLoS Med. 2017 Jan 3;14(1):e1002191. doi: 10.1371/journal.pmed.1002191. eCollection 2017 Jan.
Abstract
Matthew Herder suggests it may be time to re-examine the purpose of the U.S. Orphan Drug Act.
摘要
马修·赫德认为，或许是时候重新审视美国《孤儿药法案》的目的了。
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本文引用的文献
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Biomarker-Defined Subsets of Common Diseases: Policy and Economic Implications of Orphan Drug Act Coverage.生物标志物定义的常见疾病亚组：《孤儿药法案》覆盖范围的政策与经济影响
PLoS Med. 2017 Jan 3;14(1):e1002190. doi: 10.1371/journal.pmed.1002190. eCollection 2017 Jan.
2
Orphan drug incentives in the pharmacogenomic context: policy responses in the US and Canada.药物基因组学背景下的罕见病药物激励措施：美国和加拿大的政策回应
J Law Biosci. 2015 Apr 19;2(2):263-291. doi: 10.1093/jlb/lsv013. eCollection 2015 Jul.
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Funding innovation for treatment for rare diseases: adopting a cost-based yardstick approach.为罕见病治疗创新提供资金：采用基于成本的衡量标准方法。
Orphanet J Rare Dis. 2013 Nov 16;8:180. doi: 10.1186/1750-1172-8-180.
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Orphan drug regulations. Final rule.孤儿药法规。最终规则。
Fed Regist. 2013 Jun 12;78(113):35117-35.
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Paying for the Orphan Drug System: break or bend? Is it time for a new evaluation system for payers in Europe to take account of new rare disease treatments?支付孤儿药系统费用：是坚持还是妥协？是否到了欧洲的支付方采用新的评估体系来考虑新的罕见病治疗方法的时候了？
Orphanet J Rare Dis. 2012 Sep 26;7:74. doi: 10.1186/1750-1172-7-74.
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