Department of Medicine, Hematology and Oncology Division, Weill Cornell Medicine, New York, New York 10065, USA.
Neuroimmunomodulation and Molecular Oncology Department, Institute for Biomedical Research (BIOMED), National Research Council of Argentina (CONICET), Catholic University of Argentina (UCA), C1107AFB Ciudad Autonoma de Buenos Aires, Argentina.
Nat Commun. 2017 Jan 30;8:14290. doi: 10.1038/ncomms14290.
Peripheral T-cell lymphomas (PTCL) are aggressive diseases with poor response to chemotherapy and dismal survival. Identification of effective strategies to target PTCL biology represents an urgent need. Here we report that PTCL are sensitive to transcription-targeting drugs, and, in particular, to THZ1, a covalent inhibitor of cyclin-dependent kinase 7 (CDK7). The STAT-signalling pathway is highly vulnerable to THZ1 even in PTCL cells that carry the activating STAT3 mutation Y640F. In mutant cells, CDK7 inhibition decreases STAT3 chromatin binding and expression of highly transcribed target genes like MYC, PIM1, MCL1, CD30, IL2RA, CDC25A and IL4R. In surviving cells, THZ1 decreases the expression of STAT-regulated anti-apoptotic BH3 family members MCL1 and BCL-XL sensitizing PTCL cells to BH3 mimetic drugs. Accordingly, the combination of THZ1 and the BH3 mimetic obatoclax improves lymphoma growth control in a primary PTCL ex vivo culture and in two STAT3-mutant PTCL xenografts, delineating a potential targeted agent-based therapeutic option for these patients.
外周 T 细胞淋巴瘤(PTCL)是侵袭性疾病,对化疗反应差,生存预后差。寻找针对 PTCL 生物学的有效治疗策略是当务之急。本研究报告称,PTCL 对转录靶向药物敏感,特别是 THZ1,一种细胞周期蛋白依赖性激酶 7(CDK7)的共价抑制剂。STAT 信号通路对 THZ1非常敏感,即使在携带激活 STAT3 突变 Y640F 的 PTCL 细胞中也是如此。在突变细胞中,CDK7 抑制降低了 STAT3 染色质结合和高度转录靶基因的表达,如 MYC、PIM1、MCL1、CD30、IL2RA、CDC25A 和 IL4R。在存活细胞中,THZ1 降低了 STAT 调节的抗凋亡 BH3 家族成员 MCL1 和 BCL-XL 的表达,使 PTCL 细胞对 BH3 模拟药物敏感。因此,THZ1 和 BH3 模拟药物 obatoclax 的联合应用改善了原发性 PTCL 体外培养和两种 STAT3 突变型 PTCL 异种移植中的淋巴瘤生长控制,为这些患者提供了一种潜在的靶向药物治疗选择。