School of Life Science, Beijing Institute of Technology, Beijing, 100081, People's Republic of China.
Mol Neurobiol. 2018 May;55(5):3841-3855. doi: 10.1007/s12035-017-0606-3. Epub 2017 May 25.
γ-Secretase has been a therapeutical target for its key role in cleaving APP to generate β-amyloid (Aβ), the primary constituents of senile plaques and a hallmark of Alzheimer's disease (AD) pathology. Recently, γ-secretase-associating proteins showed promising role in specifically modulating APP processing while sparing Notch signaling; however, the underlying mechanism is still unclear. A co-immunoprecipitation (Co-IP) coupled with mass spectrometry proteomic assay for Presenilin1 (PS1, the catalytic subunit of γ-secretase) was firstly conducted to find more γ-secretase-associating proteins. Gene ontology analysis of these results identified Rab21 as a potential PS1 interacting protein, and the interaction between them was validated by reciprocal Co-IP and immunofluorescence assay. Then, molecular and biochemical methods were used to investigate the effect of Rab21 on APP processing. Results showed that overexpression of Rab21 enhanced Aβ generation, while silencing of Rab21 reduced the accumulation of Aβ, which resulted due to change in γ-secretase activity rather than α- or β-secretase. Finally, we demonstrated that Rab21 had no effect on γ-secretase complex synthesis or metabolism but enhanced PS1 endocytosis and translocation to late endosome/lysosome. In conclusion, we identified a novel γ-secretase-associating protein Rab21 and illustrate that Rab21 promotes γ-secretase internalization and translocation to late endosome/lysosome. Moreover, silencing of Rab21 decreases the γ-secretase activity in APP processing thus production of Aβ. All these results open new gateways towards the understanding of γ-secretase-associating proteins in APP processing and make inhibition of Rab21 a promising strategy for AD therapy.
γ-分泌酶在切割 APP 以产生β-淀粉样蛋白(Aβ)方面发挥着关键作用,Aβ 是老年斑的主要成分,也是阿尔茨海默病(AD)病理学的标志。最近,γ-分泌酶相关蛋白在特异性调节 APP 加工而不影响 Notch 信号方面显示出有希望的作用;然而,其潜在机制尚不清楚。首先进行了一种共免疫沉淀(Co-IP)与质谱蛋白质组学测定法,用于鉴定早老素 1(PS1,γ-分泌酶的催化亚基)的 γ-分泌酶相关蛋白。对这些结果的基因本体分析鉴定 Rab21 是 PS1 的潜在相互作用蛋白,并通过相互 Co-IP 和免疫荧光测定验证了它们之间的相互作用。然后,使用分子和生化方法研究 Rab21 对 APP 加工的影响。结果表明,Rab21 的过表达增强了 Aβ 的产生,而 Rab21 的沉默减少了 Aβ 的积累,这是由于 γ-分泌酶活性的变化而不是 α-或 β-分泌酶的变化所致。最后,我们证明 Rab21 对 γ-分泌酶复合物的合成或代谢没有影响,但增强了 PS1 的内吞作用和向晚期内体/溶酶体的易位。总之,我们鉴定了一种新的 γ-分泌酶相关蛋白 Rab21,并表明 Rab21 促进 γ-分泌酶的内化和向晚期内体/溶酶体的易位。此外,Rab21 的沉默减少了 APP 加工中的 γ-分泌酶活性,从而减少了 Aβ 的产生。所有这些结果为理解 APP 加工中的 γ-分泌酶相关蛋白开辟了新的途径,并使抑制 Rab21 成为治疗 AD 的一种有前途的策略。