Future of Rare Diseases Research 2017-2027: An IRDiRC Perspective.
作者信息
Austin Christopher P, Cutillo Christine M, Lau Lilian P L, Jonker Anneliene H, Rath Ana, Julkowska Daria, Thomson David, Terry Sharon F, de Montleau Béatrice, Ardigò Diego, Hivert Virginie, Boycott Kym M, Baynam Gareth, Kaufmann Petra, Taruscio Domenica, Lochmüller Hanns, Suematsu Makoto, Incerti Carlo, Draghia-Akli Ruxandra, Norstedt Irene, Wang Lu, Dawkins Hugh J S
机构信息
National Center for Advancing Translational Sciences (NCATS), National Institutes of Health (NIH), Bethesda, Maryland, USA.
IRDiRC Scientific Secretariat, Inserm-US14, Rare Diseases Platform, Paris, France.
出版信息
Clin Transl Sci. 2018 Jan;11(1):21-27. doi: 10.1111/cts.12500. Epub 2017 Oct 23.
Abstract
摘要
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