Esatoglu Sinem Nihal, Hatemi Gulen, Ugurlu Serdal, Gokturk Aycan, Tascilar Koray, Ozdogan Huri
Division of Rheumatology, Department of Internal Medicine, Cerrahpasa Medical School, Istanbul University Department of Internal Medicine, Cerrahpasa Medical School, Istanbul University, Istanbul, Turkey.
Medicine (Baltimore). 2017 Aug;96(34):e7859. doi: 10.1097/MD.0000000000007859.
There are no treatment modalities, which were proven to prevent the deposition of amyloid, proteinuria, and loss of renal function due to amyloidosis. Anti-tumor necrosis factor agents (anti-TNFs) were shown to decrease the production of serum amyloid A protein.We aimed to evaluate the long-term efficacy and safety of anti-TNFs in secondary (AA) amyloidosis patients treated in a single center.Thirty-seven patients with AA amyloidosis were started an anti-TNF for AA amyloidosis between March 2001 and June 2008 and followed until May 2016 unless deceased. They were surveyed for the endpoints of death, development of end-stage renal disease (ESRD), switch to another agent due to worsening of amyloidosis and adverse events.Among the 37 patients, 12 (32%) had died, 9 (24%) had ESRD, and 8 (22%) had started another group of biologic due to worsening of amyloidosis indicated by an increase in proteinuria, 5 (14%) patients are still doing well with anti-TNFs, and 3 (8%) are off treatment at the end of a median follow-up of 10 (interquartile range [IQR]: 5.5-10.5) years since the start of anti-TNFs and 10 (IQR: 8-13) years since the diagnosis of AA amyloidosis. Most common serious adverse events were sepsis and thrombotic events observed in 8 and 4 patients, respectively.Treatment with anti-TNFs may be associated with a higher survival rate compared with historic cohorts of AA amyloidosis, especially when started early with a lower serum creatinine level at baseline. Caution is needed regarding serious adverse events, especially infections.
目前尚无经证实可预防淀粉样变性所致淀粉样蛋白沉积、蛋白尿和肾功能丧失的治疗方法。抗肿瘤坏死因子药物(抗TNFs)已显示可减少血清淀粉样蛋白A的产生。我们旨在评估在单一中心接受治疗的继发性(AA型)淀粉样变性患者中抗TNFs的长期疗效和安全性。2001年3月至2008年6月期间,37例AA型淀粉样变性患者开始接受抗TNFs治疗AA型淀粉样变性,除非死亡,否则随访至2016年5月。对患者进行了死亡、终末期肾病(ESRD)进展、因淀粉样变性恶化而改用其他药物以及不良事件等终点指标的调查。在这37例患者中,12例(32%)死亡,9例(24%)发生ESRD,8例(22%)因蛋白尿增加提示淀粉样变性恶化而开始使用另一组生物制剂,5例(14%)患者使用抗TNFs治疗效果仍然良好,3例(8%)在自开始使用抗TNFs起中位随访10年(四分位间距[IQR]:5.5 - 10.5)以及自诊断AA型淀粉样变性起10年(IQR:8 - 13)时停止治疗。最常见的严重不良事件分别为8例患者发生的败血症和4例患者发生的血栓形成事件。与AA型淀粉样变性的历史队列相比,抗TNFs治疗可能与更高的生存率相关,尤其是在基线血清肌酐水平较低时早期开始治疗。对于严重不良事件,尤其是感染,需要谨慎对待。