Huang Ching-Ying, Ho Ming-Ching, Lee Jia-Jung, Hwang Daw-Yang, Ko Hui-Wen, Cheng Yu-Che, Hsu Yu-Hung, Lu Huai-En, Chen Hung-Chun, Hsieh Patrick C H
Institute of Biomedical Sciences, Academia Sinica, Taipei, Taiwan.
Ph.D. Program in Translational Medicine, Kaohsiung Medical University and Academia Sinica, Taiwan; Division of Nephrology, Department of Internal Medicine, Kaohsiung Medical University Hospital, Kaohsiung Medical University, Kaohsiung, Taiwan; Faculty of Medicine, College of Medicine, Kaohsiung Medical University, Kaohsiung, Taiwan; Faculty of Renal Care, College of Medicine, Kaohsiung Medical University, Kaohsiung, Taiwan.
Stem Cell Res. 2017 Oct;24:139-143. doi: 10.1016/j.scr.2017.09.004. Epub 2017 Sep 15.
Autosomal dominant polycystic kidney disease is one of the most prevalent forms of inherited cystic kidney disease, and can be characterized by kidney cyst formation and enlargement. Here we report the generation of a Type 1 ADPKD disease iPS cell line, IBMS-iPSC-012-12, which retains the conserved deletion of PKD1, normal karyotype and exhibits the properties of pluripotent stem cells such as ES-like morphology, expression of pluripotent markers and capacity to differentiate into all three germ layers. Our results show that we have successfully generated a patient-specific iPS cell line with a mutation in PKD1 for study of renal disease pathophysiology.
常染色体显性多囊肾病是遗传性囊性肾病最常见的形式之一,其特征为肾囊肿的形成和增大。在此,我们报告了1型常染色体显性多囊肾病疾病诱导多能干细胞系IBMS-iPSC-012-12的产生,该细胞系保留了PKD1基因的保守缺失、正常核型,并表现出多能干细胞的特性,如类胚胎干细胞形态、多能性标志物的表达以及分化为所有三个胚层的能力。我们的结果表明,我们已成功生成了一个携带PKD1基因突变的患者特异性诱导多能干细胞系,用于研究肾脏疾病的病理生理学。