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International Workshop:: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16-18 November 2016, Rome, Italy.

作者信息

Mancuso Michelangelo, McFarland Robert, Klopstock Thomas, Hirano Michio

机构信息

Department of Experimental and Clinical Medicine, Neurological Institute, University of Pisa, Italy.

Wellcome Trust Centre for Mitochondrial Research, Institute of Genetic Medicine, Department of Physiology and Functional Genomics NE1 3BZ, Newcastle University, Newcastle upon Tyne, UK.

出版信息

Neuromuscul Disord. 2017 Dec;27(12):1126-1137. doi: 10.1016/j.nmd.2017.08.006. Epub 2017 Sep 8.

DOI:10.1016/j.nmd.2017.08.006
PMID:29074296
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC6094160/
Abstract
摘要

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JIMD Rep. 2017;36:7-17. doi: 10.1007/8904_2016_35. Epub 2017 Jan 17.
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