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New Treatments on the Horizon for Familial Hypercholesterolemia.

作者信息

Al-Rasadi Khalid, Al-Waili Khalid

机构信息

Department of Biochemistry, Sultan Qaboos University Hospital, Muscat, Oman.

出版信息

Oman Med J. 2017 Nov;32(6):447-448. doi: 10.5001/omj.2017.86.

DOI:10.5001/omj.2017.86
PMID:29218118
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC5702991/
Abstract
摘要

相似文献

1
New Treatments on the Horizon for Familial Hypercholesterolemia.家族性高胆固醇血症即将出现的新疗法。
Oman Med J. 2017 Nov;32(6):447-448. doi: 10.5001/omj.2017.86.
2
What is new in familial hypercholesterolemia?家族性高胆固醇血症有哪些新进展?
Curr Opin Lipidol. 2014 Jun;25(3):183-8. doi: 10.1097/MOL.0000000000000073.
3
Toward a new clinical classification of patients with familial hypercholesterolemia: One perspective from Spain.从西班牙角度探讨家族性高胆固醇血症患者的新型临床分类。
Atherosclerosis. 2019 Aug;287:89-92. doi: 10.1016/j.atherosclerosis.2019.06.905. Epub 2019 Jun 20.
4
Premature Coronary Artery Disease due to Homozygous Familial Hypercholesterolemia in a 12-Year-Old Girl.12 岁女孩因纯合子家族性高胆固醇血症导致的早发性冠状动脉疾病。
Balkan Med J. 2018 Mar 15;35(2):208-211. doi: 10.4274/balkanmedj.2017.0490. Epub 2017 Oct 26.
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Does intrauterine exposure to hypercholesterolemia adversely affect familial hypercholesterolemia phenotype?子宫内暴露于高胆固醇血症是否会对家族性高胆固醇血症表型产生不利影响?
Curr Opin Lipidol. 2016 Aug;27(4):382-7. doi: 10.1097/MOL.0000000000000299.
6
Screening and management of familial hypercholesterolemia.家族性高胆固醇血症的筛查和管理。
Curr Opin Cardiol. 2019 Sep;34(5):526-530. doi: 10.1097/HCO.0000000000000660.
7
A systematic review of current studies in patients with familial hypercholesterolemia by use of national familial hypercholesterolemia registries.一项利用国家家族性高胆固醇血症登记系统对家族性高胆固醇血症患者当前研究的系统评价。
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Monogenic, polygenic, and oligogenic familial hypercholesterolemia.单基因、多基因和寡基因家族性高胆固醇血症。
Curr Opin Lipidol. 2019 Aug;30(4):300-306. doi: 10.1097/QCO.0000000000000563.
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Familial hypercholesterolemia: experience from the French-Canadian population.家族性高胆固醇血症:来自法裔加拿大人群的经验。
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本文引用的文献

1
Anti-PCSK9 antibodies for the treatment of heterozygous familial hypercholesterolemia: patient selection and perspectives.用于治疗杂合子家族性高胆固醇血症的抗PCSK9抗体:患者选择与展望
Vasc Health Risk Manag. 2017 Sep 4;13:343-351. doi: 10.2147/VHRM.S130338. eCollection 2017.
2
Knowns and unknowns in the care of pediatric familial hypercholesterolemia.小儿家族性高胆固醇血症护理中的已知与未知因素
J Lipid Res. 2017 Sep;58(9):1765-1776. doi: 10.1194/jlr.S074039. Epub 2017 Jul 12.
3
Diagnostic Yield and Clinical Utility of Sequencing Familial Hypercholesterolemia Genes in Patients With Severe Hypercholesterolemia.对重度高胆固醇血症患者进行家族性高胆固醇血症基因测序的诊断率及临床应用价值
J Am Coll Cardiol. 2016 Jun 7;67(22):2578-89. doi: 10.1016/j.jacc.2016.03.520. Epub 2016 Apr 3.
4
ODYSSEY FH I and FH II: 78 week results with alirocumab treatment in 735 patients with heterozygous familial hypercholesterolaemia.ODYSSEY FH I和FH II:735例杂合子家族性高胆固醇血症患者接受阿利西尤单抗治疗78周的结果
Eur Heart J. 2015 Nov 14;36(43):2996-3003. doi: 10.1093/eurheartj/ehv370. Epub 2015 Sep 1.
5
Identification and Treatment of Patients with Homozygous Familial Hypercholesterolaemia: Information and Recommendations from a Middle East Advisory Panel.纯合子家族性高胆固醇血症患者的识别与治疗:中东咨询小组的信息与建议
Curr Vasc Pharmacol. 2015;13(6):759-70. doi: 10.2174/1570161113666150827125040.
6
Familial hypercholesterolaemia in children and adolescents: gaining decades of life by optimizing detection and treatment.儿童和青少年家族性高胆固醇血症:通过优化检测与治疗延长数十年寿命
Eur Heart J. 2015 Sep 21;36(36):2425-37. doi: 10.1093/eurheartj/ehv157. Epub 2015 May 25.
7
PCSK9 inhibition with evolocumab (AMG 145) in heterozygous familial hypercholesterolaemia (RUTHERFORD-2): a randomised, double-blind, placebo-controlled trial.依洛尤单抗(AMG 145)抑制载脂蛋白 B 代谢通路治疗杂合子家族性高胆固醇血症(RUTHERFORD-2):一项随机、双盲、安慰剂对照试验。
Lancet. 2015 Jan 24;385(9965):331-40. doi: 10.1016/S0140-6736(14)61399-4. Epub 2014 Oct 1.
8
Homozygous familial hypercholesterolaemia: new insights and guidance for clinicians to improve detection and clinical management. A position paper from the Consensus Panel on Familial Hypercholesterolaemia of the European Atherosclerosis Society.纯合子家族性高胆固醇血症:临床医生提高检测和临床管理水平的新见解与指南。欧洲动脉粥样硬化学会家族性高胆固醇血症共识小组的立场文件。
Eur Heart J. 2014 Aug 21;35(32):2146-57. doi: 10.1093/eurheartj/ehu274. Epub 2014 Jul 22.
9
Familial hypercholesterolemia: A review.家族性高胆固醇血症:综述
Ann Pediatr Cardiol. 2014 May;7(2):107-17. doi: 10.4103/0974-2069.132478.
10
Familial hypercholesterolaemia is underdiagnosed and undertreated in the general population: guidance for clinicians to prevent coronary heart disease: consensus statement of the European Atherosclerosis Society.家族性高胆固醇血症在普通人群中漏诊和治疗不足:预防冠心病的临床医生指南:欧洲动脉粥样硬化学会共识声明。
Eur Heart J. 2013 Dec;34(45):3478-90a. doi: 10.1093/eurheartj/eht273. Epub 2013 Aug 15.