Medical Clinic and Policlinic 1, Hematology and Cellular Therapy, Leipzig University Hospital, Leipzig, Germany.
European Myelodysplastic Syndromes Cooperative Group (EMSCO Group), Leipzig, Germany.
Blood. 2019 Mar 7;133(10):1020-1030. doi: 10.1182/blood-2018-06-857102. Epub 2018 Nov 7.
The heterogeneity of myelodysplastic syndromes (MDSs) has made evaluating patient response to treatment challenging. In 2006, the International Working Group (IWG) proposed a revision to previously published standardized response criteria (IWG 2000) for uniformly evaluating clinical responses in MDSs. These IWG 2006 criteria have been used prospectively in many clinical trials in MDSs, but proved challenging in several of them, especially for the evaluation of erythroid response. In this report, we provide rationale for modifications (IWG 2018) of these recommendations, mainly for "hematological improvement" criteria used for lower-risk MDSs, based on recent practical and reported experience in clinical trials. Most suggestions relate to erythroid response assessment, which are refined in an overall more stringent manner. Two major proposed changes are the differentiation between "procedures" and "criteria" for hematologic improvement-erythroid assessment and a new categorization of transfusion-burden subgroups.
骨髓增生异常综合征 (MDS) 的异质性使得评估患者对治疗的反应变得具有挑战性。2006 年,国际工作组 (IWG) 对之前发表的标准化反应标准 (IWG 2000) 进行了修订,以便在 MDS 中统一评估临床反应。这些 IWG 2006 标准已在 MDS 的许多临床试验中前瞻性使用,但在其中一些临床试验中证明具有挑战性,尤其是在评估红细胞反应方面。在本报告中,我们根据临床试验中的近期实践和报告经验,为这些建议的修改(IWG 2018)提供了理由,主要是针对低危 MDS 所用的“血液学改善”标准。大多数建议都与红细胞反应评估有关,这些建议在整体上更加严格。两个主要的建议变化是区分用于红细胞评估的血液学改善的“程序”和“标准”,以及输血负担亚组的新分类。