Hoepfner Dominic, McAllister Gregory, Hoffman Gregory R
Novartis Institutes for BioMedical Research, Novartis Pharma AG, Basel, Switzerland.
Novartis Institutes for BioMedical Research, Cambridge, MA, USA.
Methods Mol Biol. 2019;1888:153-174. doi: 10.1007/978-1-4939-8891-4_9.
Chemogenomic profiling is a powerful and unbiased approach to elucidate pharmacological targets and the mechanism of bioactive compounds. It is based on identifying cellular hypersensitivity and resistance caused by individual gene modulations with genome-wide coverage. Due to the requirement of bar-coded, genome-wide deletion collections, high-resolution experiments of this nature have historically been limited to fungal systems. Pooled RNAi reagents have enabled similar attempts in mammalian cells but efforts have been hampered by significant off-target effects and experimental noise. The CRISPR/Cas9 system for the first time enables precise DNA editing at defined loci in a genome-wide fashion. Here we present the detailed protocol that leverages the CRISPR/Cas9 system for chemogenomic profiling and target identification of diverse chemical probes.
化学基因组学分析是一种强大且无偏倚的方法,用于阐明药理靶点和生物活性化合物的作用机制。它基于识别由全基因组覆盖的单个基因调控引起的细胞超敏反应和抗性。由于需要条形码化的全基因组缺失文库,这种高分辨率实验在历史上一直局限于真菌系统。汇集的RNAi试剂已在哺乳动物细胞中进行了类似尝试,但由于显著的脱靶效应和实验噪音而受到阻碍。CRISPR/Cas9系统首次实现了在全基因组范围内对特定基因座进行精确的DNA编辑。在此,我们展示了利用CRISPR/Cas9系统进行化学基因组学分析和鉴定多种化学探针靶点的详细方案。