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Gene therapy for retinal dystrophy.

作者信息

Sahel José Alain, Dalkara Deniz

机构信息

Department of Ophthalmology, University of Pittsburgh School of Medicine, Pittsburgh, PA, USA.

Institut de la Vision, Sorbonne Université, INSERM, CNRS, Paris, France.

出版信息

Nat Med. 2019 Feb;25(2):198-199. doi: 10.1038/s41591-019-0346-1.

DOI:10.1038/s41591-019-0346-1

PMID:30718907

Abstract

摘要

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相似文献

Gene therapy for retinal dystrophy.

Nat Med. 2019 Feb;25(2):198-199. doi: 10.1038/s41591-019-0346-1.

[Genotype screening of retinal dystrophies in the Japanese population using a microarray].

Nippon Ganka Gakkai Zasshi. 2013 Jan;117(1):12-8.

Screening of SPATA7 in patients with Leber congenital amaurosis and severe childhood-onset retinal dystrophy reveals disease-causing mutations.

Invest Ophthalmol Vis Sci. 2011 May 9;52(6):3032-8. doi: 10.1167/iovs.10-7025.

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Adv Exp Med Biol. 2019;1185:71-77. doi: 10.1007/978-3-030-27378-1_12.

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Gene Ther. 2012 Feb;19(2):154-61. doi: 10.1038/gt.2011.161. Epub 2011 Oct 27.

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Middle East Afr J Ophthalmol. 2016 Jan-Mar;23(1):139-41. doi: 10.4103/0974-9233.171779.

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Hum Gene Ther Clin Dev. 2015 Mar;26(1):15-26. doi: 10.1089/humc.2014.155. Epub 2015 Feb 11.

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