T-cell replete haploidentical bone marrow transplantation and post-transplant cyclophosphamide for patients with inborn errors.
作者信息
Kurzay Mathias, Hauck Fabian, Schmid Irene, Wiebking Volker, Eichinger Anna, Jung Eva, Boekstegers Ann, Feuchtinger Tobias, Klein Christoph, Albert Michael H
机构信息
Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, Ludwig-Maximilians Universität, Munich, Germany.
Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, Ludwig-Maximilians Universität, Munich, Germany
出版信息
Haematologica. 2019 Oct;104(10):e478-e482. doi: 10.3324/haematol.2018.215285. Epub 2019 Mar 7.
Abstract
摘要
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Biol Blood Marrow Transplant. 2018 Mar;24(3):529-536. doi: 10.1016/j.bbmt.2017.11.009. Epub 2017 Nov 16.
2
Reduced-toxicity alternate-donor stem cell transplantation with posttransplant cyclophosphamide for primary immunodeficiency disorders.采用移植后环磷酰胺的低毒性替代供体干细胞移植治疗原发性免疫缺陷病。
Pediatr Blood Cancer. 2018 Jan;65(1). doi: 10.1002/pbc.26783. Epub 2017 Sep 13.
3
T-cell receptor αβ and CD19 cell-depleted haploidentical and mismatched hematopoietic stem cell transplantation in primary immune deficiency.T 细胞受体 αβ 和 CD19 细胞耗竭的半相合和不合造血干细胞移植治疗原发性免疫缺陷。
J Allergy Clin Immunol. 2018 Apr;141(4):1417-1426.e1. doi: 10.1016/j.jaci.2017.07.008. Epub 2017 Aug 3.
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Diagnosis and severity criteria for sinusoidal obstruction syndrome/veno-occlusive disease in pediatric patients: a new classification from the European society for blood and marrow transplantation.儿童患者窦状隙阻塞综合征/静脉阻塞性疾病的诊断和严重程度标准：来自欧洲血液和骨髓移植学会的新分类。
Bone Marrow Transplant. 2018 Feb;53(2):138-145. doi: 10.1038/bmt.2017.161. Epub 2017 Jul 31.
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Reduced toxicity, myeloablative HLA-haploidentical hematopoietic stem cell transplantation with post-transplantation cyclophosphamide for sickle cell disease.降低毒性的清髓性人类白细胞抗原半相合造血干细胞移植联合移植后环磷酰胺治疗镰状细胞病
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