Department of Radiation and Cellular Oncology, University of Chicago, Chicago, IL, 60637, USA.
StarWise Therapeutics LLC, Madison, WI, 53719, USA.
ChemMedChem. 2019 May 17;14(10):1031-1040. doi: 10.1002/cmdc.201900075. Epub 2019 Apr 17.
RAD51 is the central protein in homologous recombination (HR) repair, where it first binds ssDNA and then catalyzes strand invasion via a D-loop intermediate. Additionally, RAD51 plays a role in faithful DNA replication by protecting stalled replication forks; this requires RAD51 to bind DNA but may not require the strand invasion activity of RAD51. We previously described a small-molecule inhibitor of RAD51 named RI(dl)-2 (RAD51 inhibitor of D-loop formation #2, hereafter called 2 h), which inhibits D-loop activity while sparing ssDNA binding. However, 2 h is limited in its ability to inhibit HR in vivo, preventing only about 50 % of total HR events in cells. We sought to improve upon this by performing a structure-activity relationship (SAR) campaign for more potent analogues of 2 h. Most compounds were prepared from 1-(2-aminophenyl)pyrroles by forming the quinoxaline moiety either by condensation with aldehydes, then dehydrogenation of the resulting 4,5-dihydro intermediates, or by condensation with N,N'-carbonyldiimidazole, chlorination, and installation of the 4-substituent through Suzuki-Miyaura coupling. Many analogues exhibited enhanced activity against human RAD51, but in several of these compounds the increased inhibition was due to the introduction of dsDNA intercalation activity. We developed a sensitive assay to measure dsDNA intercalation, and identified two analogues of 2 h that promote complete HR inhibition in cells while exerting minimal intercalation activity.
RAD51 是同源重组 (HR) 修复的核心蛋白,它首先与单链 DNA 结合,然后通过 D 环中间体催化链入侵。此外,RAD51 在忠实的 DNA 复制中发挥作用,通过保护停滞的复制叉;这需要 RAD51 结合 DNA,但可能不需要 RAD51 的链入侵活性。我们之前描述了一种名为 RI(dl)-2(D 环形成的 RAD51 抑制剂 #2,以下简称 2h)的 RAD51 小分子抑制剂,它抑制 D 环活性,同时保留 ssDNA 结合。然而,2h 在体内抑制 HR 的能力有限,只能阻止细胞中约 50%的总 HR 事件。我们通过对 2h 的更有效的类似物进行构效关系 (SAR) 研究来改进这一点。大多数化合物是通过形成喹喔啉部分,要么通过与醛缩合,然后将得到的 4,5-二氢中间体脱氢,要么通过与 N,N'-碳酰二咪唑缩合、氯化,然后通过铃木-宫浦偶联将 4-取代基安装在 1-(2-氨基苯基)吡咯上来制备的。许多类似物对人 RAD51 的活性增强,但在其中一些化合物中,抑制活性的增加是由于引入了双链 DNA 插入活性。我们开发了一种灵敏的测定法来测量双链 DNA 插入,鉴定了两种类似物 2h,它们在细胞中完全抑制 HR 而发挥最小的插入活性。