Sirolimus in lymphangioleiomyomatosis: A case in point for research in 'orphan' diseases.
作者信息
Koul Parvaiz A, Mehfooz Nazia
机构信息
Department of Internal and Pulmonary Medicine, Sheri Kashmir Institute of Medical Sciences, Srinagar, Jammu and Kashmir, India.
Department of Pulmonary Medicine, Sheri Kashmir Institute of Medical Sciences, Srinagar, Jammu and Kashmir, India.
出版信息
Lung India. 2019 Jul-Aug;36(4):353-355. doi: 10.4103/lungindia.lungindia_280_19.
Abstract
摘要
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Pulmonary lymphangioleiomyomatosis presenting as spontaneous pneumothorax treated with sirolimus - A case report.以自发性气胸为表现的肺淋巴管平滑肌瘤病经西罗莫司治疗——病例报告
Lung India. 2018 Mar-Apr;35(2):154-156. doi: 10.4103/lungindia.lungindia_60_17.
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Lung function response and side effects to rapamycin for lymphangioleiomyomatosis: a prospective national cohort study.肺功能对雷帕霉素治疗淋巴管肌瘤病的反应和副作用：一项前瞻性全国队列研究。
Thorax. 2018 Apr;73(4):369-375. doi: 10.1136/thoraxjnl-2017-210872. Epub 2017 Oct 9.
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Lymphangioleiomyomatosis: A Monogenic Model of Malignancy.淋巴管平滑肌瘤病：一种恶性肿瘤的单基因模型。
Annu Rev Med. 2017 Jan 14;68:69-83. doi: 10.1146/annurev-med-050715-104245.
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Interstitial Lung Disease in India. Results of a Prospective Registry.印度间质性肺病。一项前瞻性登记研究结果。
Am J Respir Crit Care Med. 2017 Mar 15;195(6):801-813. doi: 10.1164/rccm.201607-1484OC.
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The changing face of a rare disease: lymphangioleiomyomatosis.罕见病的变化面貌：淋巴管平滑肌瘤病。
Eur Respir J. 2015 Nov;46(5):1471-85. doi: 10.1183/13993003.00412-2015. Epub 2015 Sep 24.
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