Department of Haematology, Wellcome & MRC Cambridge Stem Cell Institute, Cambridge, UK.
Wellcome Trust Sanger Institute, Hinxton, Cambridge, UK.
Exp Hematol. 2019 Aug;76:1-12.e5. doi: 10.1016/j.exphem.2019.07.003. Epub 2019 Jul 18.
Pluripotent stem cell (PSC) differentiation in vitro represents a powerful and tractable model to study mammalian development and an unlimited source of cells for regenerative medicine. Within hematology, in vitro PSC hematopoiesis affords novel insights into blood formation and represents an exciting potential approach to generate hematopoietic and immune cell types for transplantation and transfusion. Most studies to date have focused on in vitro hematopoiesis from mouse PSCs and human PSCs. However, differences in mouse and human PSC culture protocols have complicated the translation of discoveries between these systems. We recently developed a novel chemical media formulation, expanded potential stem cell medium (EPSCM), that maintains mouse PSCs in a unique cellular state and extraembryonic differentiation capacity. Herein, we describe how EPSCM can be directly used to stably maintain human PSCs. We further demonstrate that human PSCs maintained in EPSCM can spontaneously form embryoid bodies and undergo in vitro hematopoiesis using a simple differentiation protocol, similar to mouse PSC differentiation. EPSCM-maintained human PSCs generated at least two hematopoietic cell populations, which displayed distinct transcriptional profiles by RNA-sequencing (RNA-seq) analysis. EPSCM also supports gene targeting using homologous recombination, affording generation of an SPI1 (PU.1) reporter PSC line to study and track in vitro hematopoiesis. EPSCM therefore provides a useful tool not only to study pluripotency but also hematopoietic cell specification and developmental-lineage commitment.
多能干细胞(PSC)的体外分化代表了研究哺乳动物发育的强大且可行的模型,也是再生医学中无限细胞来源的方法。在血液学领域,体外 PSC 造血为血液形成提供了新的见解,并代表了一种令人兴奋的潜在方法,可以生成用于移植和输血的造血和免疫细胞类型。迄今为止,大多数研究都集中在来自小鼠 PSCs 和人 PSCs 的体外造血上。然而,小鼠和人 PSC 培养方案的差异使得这些系统之间的发现难以转化。我们最近开发了一种新的化学培养基配方,即扩展潜能干细胞培养基(EPSCM),它可以维持小鼠 PSCs 处于独特的细胞状态和胚外分化能力。在此,我们描述了如何直接使用 EPSCM 来稳定维持人 PSCs。我们进一步证明,在 EPSCM 中维持的人 PSCs 可以自发形成类胚体,并通过简单的分化方案进行体外造血,类似于小鼠 PSC 分化。使用 RNA 测序(RNA-seq)分析,EPSCM 维持的人 PSCs 至少产生了两种造血细胞群体,它们表现出不同的转录谱。EPSCM 还支持同源重组的基因靶向,从而产生 SPI1(PU.1)报告 PSC 系,以研究和跟踪体外造血。因此,EPSCM 不仅提供了研究多能性的有用工具,还提供了研究造血细胞特化和发育谱系决定的有用工具。