Bienta, Ltd, Chervonotkatska street 78, Kyiv, 02094, Ukraine.
Rudjer Boskovic Institute, 10000, Zagreb, Croatia.
Stem Cell Rev Rep. 2020 Apr;16(2):239-250. doi: 10.1007/s12015-020-09955-y.
Thymus regenerative therapy implementation is severely obstructed by the limited number and expansion capacity in vitro of tissue-specific thymic epithelial stem cells (TESC). Current solutions are mostly based on growth factors that can drive differentiation of pluripotent stem cells toward tissue-specific TESC. Target-specific small chemical compounds represent an alternative solution that could induce and support the clonal expansion of TESC and reversibly block their differentiation into mature cells. These compounds could be used both in the composition of culture media designed for TESC expansion in vitro, and in drugs development for thymic regeneration in vivo. It should allow reaching the ultimate objective - autologous thymic tissue regeneration in paediatric patients who had their thymus removed in the course of cardiac surgery.
胸腺再生疗法的实施受到组织特异性胸腺上皮干细胞(TESC)数量有限和体外扩增能力的严重阻碍。目前的解决方案大多基于生长因子,这些因子可以促使多能干细胞向组织特异性 TESC 分化。靶向特异性小分子化合物是一种替代解决方案,它可以诱导和支持 TESC 的克隆扩增,并可逆性地阻止其分化为成熟细胞。这些化合物可用于设计用于体外 TESC 扩增的培养基的组成中,以及用于体内胸腺再生的药物开发中。这将使我们能够实现最终目标——在因心脏手术而切除胸腺的儿科患者中实现自体胸腺组织再生。