Department of Protein Science, School of Engineering Sciences in Chemistry, Biotechnology and Health, KTH Royal Institute of Technology, Stockholm, Sweden.
Department of Medicinal Chemistry, Uppsala University, Uppsala, Sweden.
Sci Rep. 2020 Oct 23;10(1):18148. doi: 10.1038/s41598-020-74560-5.
The family of vascular endothelial growth factor (VEGF) ligands and their interactions with VEGF receptors (VEGFRs) play important roles in both pathological and physiological angiogenesis. Hence, agonistic and antagonistic ligands targeting this signaling pathway have potential for both studies on fundamental biology and for development of therapies and diagnostics. Here, we engineer VEGFR2-binding affibody molecules for increased thermostability, refolding and improved biodistribution. We designed libraries based on the original monomeric binders with the intention of reducing hydrophobicity, while retaining high affinity for VEGFR2. Libraries were displayed on bacteria and binders were isolated by fluorescence-activated cell sorting (FACS). In parallel, we used an automated sequence- and structure-based in silico algorithm to identify potentially stabilizing mutations. Monomeric variants isolated from the screening and the in silico approach, respectively, were characterized by circular dichroism spectroscopy and biosensor assays. The most promising mutations were combined into new monomeric constructs which were finally fused into a dimeric construct, resulting in a 15 °C increase in melting temperature, complete refolding capability after heat-induced denaturation, retained low picomolar affinity and improved biodistribution profile in an in vivo mouse model. These VEGFR2-binding affibody molecules show promise as candidates for further in vivo studies to assess their suitability as molecular imaging and therapeutic agents.
血管内皮生长因子(VEGF)配体家族及其与 VEGF 受体(VEGFR)的相互作用在病理性和生理性血管生成中起着重要作用。因此,针对该信号通路的激动剂和拮抗剂配体具有研究基础生物学和开发治疗方法和诊断方法的潜力。在这里,我们设计了具有更高热稳定性、重折叠能力和改善生物分布的 VEGFR2 结合亲和体分子。我们基于原始的单体结合物设计了文库,旨在降低疏水性,同时保留对 VEGFR2 的高亲和力。文库在细菌上展示,并用荧光激活细胞分选(FACS)分离结合物。同时,我们使用基于序列和结构的自动化计算算法来识别潜在的稳定化突变。从筛选和计算方法中分别分离出的单体变体,通过圆二色性光谱和生物传感器分析进行了表征。最有前途的突变被组合成新的单体构建体,最终融合成二聚体构建体,导致熔点提高 15°C,热诱导变性后完全重折叠能力,保留低皮摩尔亲和力,并改善体内小鼠模型中的生物分布特征。这些 VEGFR2 结合亲和体分子有望成为进一步体内研究的候选物,以评估它们作为分子成像和治疗剂的适用性。