Department of Neurology, The First Hospital of Jilin University, Changchun, 130021, China.
Department of Cardiology, The First Hospital of Jilin University, Changchun, 130021, China.
J Neurol. 2021 Dec;268(12):4630-4645. doi: 10.1007/s00415-020-10297-5. Epub 2020 Nov 11.
Spinocerebellar ataxias (SCAs), formerly known as autosomal dominant cerebellar ataxias (ADCAs), are a group of hereditary heterogeneous neurodegenerative diseases. Gait, progressive ataxia, dysarthria, and eye movement disorder are common symptoms of spinocerebellar ataxias. Other symptoms include peripheral neuropathy, cognitive impairment, psychosis, and seizures. Patients may lose their lives due to out of coordinated respiration and/or swallowing. Neurological signs cover pyramidal or extrapyramidal signs, spasm, ophthalmoplegia, hyperactive deep tendon reflexes, and so on. Different subtypes of SCAs present various clinical features. Spinocerebellar ataxia type 23 (SCA23), one subtype of the SCA family, is characterized by mutant prodynorphin (PDYN) gene. Based on literatures, this review details a series of SCA23, to improve a whole understanding of clinicians and point out the potential research direction of this dysfunction, including a history, pathophysiological mechanism, diagnosis and differential diagnosis, epigenetics, penetrance and prevalence, genetic counseling, treatment and prognosis.
脊髓小脑共济失调(SCA),以前称为常染色体显性小脑共济失调(ADCA),是一组遗传性异质性神经退行性疾病。步态、进行性共济失调、构音障碍和眼球运动障碍是脊髓小脑共济失调的常见症状。其他症状包括周围神经病、认知障碍、精神病和癫痫发作。患者可能因不协调的呼吸和/或吞咽而失去生命。神经系统体征包括锥体束或锥体外系体征、痉挛、眼肌麻痹、深腱反射亢进等。不同亚型的 SCA 表现出不同的临床特征。脊髓小脑共济失调 23 型(SCA23)是 SCA 家族的一个亚型,其特征是突变前原啡肽(PDYN)基因。基于文献,本综述详细介绍了一系列 SCA23,以提高临床医生的整体认识,并指出该功能障碍的潜在研究方向,包括病史、病理生理学机制、诊断和鉴别诊断、表观遗传学、外显率和患病率、遗传咨询、治疗和预后。