Department of Medical and Clinical Genetics, University of Helsinki, Helsinki, Finland.
Department of Veterinary Biosciences, University of Helsinki, Helsinki, Finland.
Hum Genet. 2021 Nov;140(11):1553-1562. doi: 10.1007/s00439-021-02259-2. Epub 2021 Feb 6.
The anterior pituitary gland secretes several endocrine hormones, essential for growth, reproduction and other basic physiological functions. Abnormal development or function of the pituitary gland leads to isolated or combined pituitary hormone deficiency (CPHD). At least 30 genes have been associated with human CPHD, including many transcription factors, such as POU1F1. CPHD occurs spontaneously also in mice and dogs. Two affected breeds have been reported in dogs: German Shepherds with a splice defect in the LHX3 gene and Karelian Bear Dogs (KBD) with an unknown genetic cause. We obtained samples from five KBDs presenting dwarfism and abnormal coats. A combined analysis of genome-wide association and next-generation sequencing mapped the disease to a region in chromosome 31 and identified a homozygous intronic variant in the fourth exon of the POU1F1 gene in the affected dogs. The identified variant, c.605-3C>A, resided in the splice region and was predicted to affect splicing. The variant's screening in three new prospective cases, related breeds, and ~ 8000 dogs from 207 breeds indicated complete segregation in KBDs with a carrier frequency of 8%, and high breed-specificity as carriers were found at a low frequency only in Lapponian Herders, a related breed. Our study establishes a novel canine model for CPHD with a candidate POU1F1 defect.
垂体前叶分泌多种内分泌激素,对生长、繁殖和其他基本生理功能至关重要。垂体发育或功能异常可导致孤立性或联合性垂体激素缺乏症(CPHD)。至少有 30 个基因与人类 CPHD 有关,包括许多转录因子,如 POU1F1。CPHD 在小鼠和犬中也自发发生。在犬中已经报道了两种受影响的品种:LHX3 基因剪接缺陷的德国牧羊犬和原因不明的遗传的 Karelian 熊犬(KBD)。我们从 5 只表现为矮小症和异常被毛的 KBD 中获得了样本。全基因组关联分析和下一代测序的联合分析将该疾病定位到染色体 31 上的一个区域,并在受影响的犬中鉴定出 POU1F1 基因第四外显子中的纯合内含子变异。鉴定出的变异,c.605-3C>A,位于剪接区,预计会影响剪接。该变异在三个新的前瞻性病例、相关品种和 207 个品种的~8000 只犬中的筛查表明,KBD 中存在完全分离,携带频率为 8%,并且仅在相关品种拉普兰牧羊犬中以低频率发现高品种特异性携带。我们的研究建立了一种新的 CPHD 犬模型,候选 POU1F1 缺陷。