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Gene Therapy for Sickle Cell Disease-A Debt to Be Paid.

作者信息

Ozuah Philip O

机构信息

Albert Einstein College of Medicine and Montefiore Medicine, Bronx, New York.

出版信息

JAMA Pediatr. 2021 Jun 1;175(6):565-566. doi: 10.1001/jamapediatrics.2020.7147.

DOI:10.1001/jamapediatrics.2020.7147
PMID:33749705
Abstract
摘要

相似文献

1
Gene Therapy for Sickle Cell Disease-A Debt to Be Paid.镰状细胞病的基因治疗——有待偿还的债务。
JAMA Pediatr. 2021 Jun 1;175(6):565-566. doi: 10.1001/jamapediatrics.2020.7147.
2
[Genetic conservation of sickle cell trait].[镰状细胞性状的遗传保守性]
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Therapeutic strategies in Sickle Cell Anemia: The past present and future.镰状细胞贫血的治疗策略:过去、现在与未来
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Genetic Therapies for Sickle Cell Disease.镰状细胞病的基因疗法
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Acceptability of prenatal diagnosis by a sample of parents of sickle cell anemia patients in Cameroon (sub-Saharan Africa).喀麦隆(撒哈拉以南非洲地区)镰状细胞贫血患者家长样本对产前诊断的接受度。
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Gene Therapy in a Patient with Sickle Cell Disease.镰状细胞病患者的基因治疗
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Gene Therapy in a Patient with Sickle Cell Disease.镰状细胞病患者的基因治疗
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Gene therapy in sickle cell disease: Possible utility and impact.镰状细胞病的基因治疗:潜在效用与影响
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Balancing benefits and burdens: a systematic review on ethical and social dimensions of gene and cell therapies for hereditary blood diseases.权衡利弊:关于遗传性血液疾病基因和细胞疗法伦理与社会层面的系统评价
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CRISPR technology in human diseases.用于人类疾病治疗的CRISPR技术。
MedComm (2020). 2024 Jul 29;5(8):e672. doi: 10.1002/mco2.672. eCollection 2024 Aug.
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Sickle cell disease and infertility risks: implications for counseling and care of affected girls and women.
镰状细胞病与不孕风险:对受影响女孩和妇女咨询与护理的启示
Expert Rev Hematol. 2024 Aug;17(8):493-504. doi: 10.1080/17474086.2024.2372320. Epub 2024 Jun 26.
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Life after sickle cell disease, is it really uhuru?镰状细胞病后的生活,真的是自由了吗?
Lancet Haematol. 2023 Dec;10(12):e946-e949. doi: 10.1016/S2352-3026(23)00306-X.
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Pharmacoecon Open. 2023 Mar;7(2):313-320. doi: 10.1007/s41669-023-00390-6. Epub 2023 Feb 11.
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Prevalence of comorbidities associated with sickle cell disease among non-elderly individuals with commercial insurance-A retrospective cohort study.非老年商业保险个体中与镰状细胞病相关的合并症患病率:一项回顾性队列研究。
PLoS One. 2022 Nov 29;17(11):e0278137. doi: 10.1371/journal.pone.0278137. eCollection 2022.
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Lifetime medical costs attributable to sickle cell disease among nonelderly individuals with commercial insurance.非老年商业保险个体中镰状细胞病的终身医疗费用。
Blood Adv. 2023 Feb 14;7(3):365-374. doi: 10.1182/bloodadvances.2021006281.
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A landscape analysis and discussion of value of gene therapies for sickle cell disease.镰状细胞病基因治疗的价值分析与探讨。
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Editing outside the body: Ex vivo gene-modification for β-hemoglobinopathy cellular therapy.体外交错编辑:用于β-地中海贫血症细胞治疗的体外基因修饰。
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