State Key Laboratory of Organ Failure Research, Department of Cell Biology, School of Basic Medical Sciences, Southern Medical University, Guangzhou 510515, China.
Guangdong Provincial Key Laboratory of Gastroenterology, Department of Gastroenterology, Nanfang Hospital, Southern Medical University, Guangzhou 510515, China.
Proc Natl Acad Sci U S A. 2021 Jul 27;118(30). doi: 10.1073/pnas.2020891118.
Tuberous sclerosis complex 1 (Tsc1) is a tumor suppressor that functions together with Tsc2 to negatively regulate the mechanistic target of rapamycin complex 1 (mTORC1) activity. Here, we show that Tsc1 has a critical role in the tight junction (TJ) formation of epithelium, independent of its role in Tsc2 and mTORC1 regulation. When an epithelial cell establishes contact with neighboring cells, Tsc1, but not Tsc2, migrates from the cytoplasm to junctional membranes, in which it binds myosin 6 to anchor the perijunctional actin cytoskeleton to β-catenin and ZO-1. In its absence, perijunctional actin cytoskeleton fails to form. In mice, intestine-specific or inducible, whole-body Tsc1 ablation disrupts adherens junction/TJ structures in intestine or skin epithelia, respectively, causing Crohn's disease-like symptoms in the intestine or psoriasis-like phenotypes on the skin. In patients with Crohn's disease or psoriasis, junctional Tsc1 levels in epithelial tissues are markedly reduced, concomitant with the TJ structure impairment, suggesting that Tsc1 deficiency may underlie TJ-related diseases. These findings establish an essential role of Tsc1 in the formation of cell junctions and underpin its association with TJ-related human diseases.
结节性硬化症复合物 1(Tsc1)是一种肿瘤抑制因子,与 Tsc2 一起负调控雷帕霉素靶蛋白复合物 1(mTORC1)的活性。在这里,我们表明 Tsc1 在上皮细胞紧密连接(TJ)的形成中起着关键作用,而与其在 Tsc2 和 mTORC1 调节中的作用无关。当上皮细胞与邻近细胞接触时,Tsc1(而非 Tsc2)从细胞质迁移到连接膜,在那里它与肌球蛋白 6 结合,将周质肌动球蛋白细胞骨架锚定到β-连环蛋白和 ZO-1。在 Tsc1 缺失的情况下,周质肌动球蛋白细胞骨架无法形成。在小鼠中,肠特异性或诱导性全身性 Tsc1 缺失分别破坏肠或皮肤上皮细胞的黏着连接/TJ 结构,导致肠中的克罗恩病样症状或皮肤的银屑病样表型。在克罗恩病或银屑病患者中,上皮组织中连接 Tsc1 的水平显著降低,同时 TJ 结构受损,提示 Tsc1 缺乏可能是 TJ 相关疾病的基础。这些发现确立了 Tsc1 在细胞连接形成中的重要作用,并为其与 TJ 相关人类疾病的关联提供了依据。