Center for Research in Perinatal Outcomes, University of Florida College of Medicine, Gainesville, Florida, USA.
Department of Physiology and Functional Genomics, University of Florida College of Medicine, Gainesville, Florida, USA.
Mol Reprod Dev. 2022 Nov;89(11):540-553. doi: 10.1002/mrd.23644. Epub 2022 Sep 12.
Fetal growth restriction (FGR) significantly contributes to neonatal and perinatal morbidity and mortality. Currently, there are no effective treatment options for FGR during pregnancy. We have developed a nanoparticle gene therapy targeting the placenta to increase expression of human insulin-like growth factor 1 (hIGF1) to correct fetal growth trajectories. Using the maternal nutrient restriction guinea pig model of FGR, an ultrasound-guided, intraplacental injection of nonviral, polymer-based hIGF1 nanoparticle containing plasmid with the hIGF1 gene and placenta-specific Cyp19a1 promotor was administered at mid-pregnancy. Sustained hIGF1 expression was confirmed in the placenta 5 days after treatment. Whilst increased hIGF1 did not change fetal weight, circulating fetal glucose concentration were 33%-67% higher. This was associated with increased expression of glucose and amino acid transporters in the placenta. Additionally, hIGF1 nanoparticle treatment increased the fetal capillary volume density in the placenta, and reduced interhaemal distance between maternal and fetal circulation. Overall, our findings, that trophoblast-specific increased expression of hIGF1 results in changes to glucose transporter expression and increases fetal glucose concentrations within a short time period, highlights the translational potential this treatment could have in correcting impaired placental nutrient transport in human pregnancies complicated by FGR.
胎儿生长受限(FGR)显著增加了新生儿和围产期的发病率和死亡率。目前,妊娠期间针对 FGR 尚无有效的治疗方法。我们开发了一种针对胎盘的纳米颗粒基因治疗方法,以增加人胰岛素样生长因子 1(hIGF1)的表达,从而纠正胎儿的生长轨迹。使用母体营养限制的豚鼠 FGR 模型,在妊娠中期进行超声引导的胎盘内注射非病毒、基于聚合物的 hIGF1 纳米颗粒,其中包含 hIGF1 基因和胎盘特异性 Cyp19a1 启动子。在治疗后 5 天,确认胎盘内持续表达 hIGF1。虽然增加 hIGF1 并没有改变胎儿体重,但循环胎儿葡萄糖浓度提高了 33%-67%。这与胎盘葡萄糖和氨基酸转运蛋白的表达增加有关。此外,hIGF1 纳米颗粒治疗增加了胎盘内的胎儿毛细血管体积密度,并减少了母体和胎儿循环之间的血液距离。总的来说,我们的研究结果表明,滋养层特异性增加 hIGF1 的表达会导致葡萄糖转运蛋白的表达发生变化,并在短时间内增加胎儿葡萄糖浓度,这突出了这种治疗方法在纠正人类妊娠合并 FGR 时胎盘营养转运受损方面的转化潜力。