Li Jiahe, Liu Lichang, Cao Haijun, Yang Mei, Sun Xin
Happy Life Tech, Boston, MA, 02494, USA.
Happy Life Tech, Shanghai, 200233, China.
Cost Eff Resour Alloc. 2023 Jan 18;21(1):7. doi: 10.1186/s12962-022-00412-w.
This article aims to summarize the development and challenges of real-world data (RWD) and real-world evidence (RWE) in China and introduce a unique opportunity for medical devices to gain accelerated regulatory approval in China by utilizing RWE generated in a free trade pilot zone "Boao Lecheng" in Hainan Province. In 2020, the National Medical Products Administration (NMPA) issued a draft guideline on the "Use of real-world data to support clinical evaluation for medical devices", suggesting that RWE derived from RWD could support clinical evaluation throughout the life cycle of a medical device. Meanwhile, the Chinese government has allowed qualified RWD collected in Boao Lecheng to support registration application of innovative medical devices and drugs in China. These medical devices and drugs should have been approved abroad, but not in China yet, and met urgent and unmet medical needs in China. The article also presents the successful story of an innovative Glaucoma drainage tube as the first medical device approved in China using RWE generated in Boao Lecheng in 2020. Although we are witnessing an increased interest in RWE, a few challenges remain, e.g., limited data accessibility and data sharing, concerns on data quality, etc. Collaborations among relevant stakeholders in the RWE research are vital to address the challenges.
本文旨在总结中国真实世界数据(RWD)和真实世界证据(RWE)的发展及挑战,并介绍一个独特的机遇,即医疗设备可利用在海南省自由贸易试验区“博鳌乐城”生成的RWE在中国获得加速监管批准。2020年,国家药品监督管理局(NMPA)发布了一份关于“利用真实世界数据支持医疗器械临床评价”的指导原则草案,表明源自RWD的RWE可在医疗器械的整个生命周期内支持临床评价。同时,中国政府已允许在博鳌乐城收集的合格RWD支持创新医疗器械和药品在中国的注册申请。这些医疗器械和药品应已在国外获批,但尚未在中国获批,且满足中国紧急和未满足的医疗需求。本文还介绍了一种创新型青光眼引流管的成功案例,它是2020年首个利用博鳌乐城生成的RWE在中国获批的医疗器械。尽管我们看到对RWE的兴趣日益增加,但仍存在一些挑战,例如数据获取和数据共享受限、对数据质量的担忧等。RWE研究中相关利益攸关方之间的合作对于应对这些挑战至关重要。