Univ. Bordeaux, CNRS, EPHE, INCIA, UMR 5287, F-33000 Bordeaux, France.
UF Biologie, Univ. Bordeaux, 33405 Talence, France.
Cells. 2023 Jan 21;12(3):391. doi: 10.3390/cells12030391.
Williams-Beuren syndrome (WBS) is a neurodevelopmental disorder caused by a chromosomic microdeletion (7q11.23). WBS has been modeled by a mouse line having a complete deletion (CD) of the equivalent mouse locus. This model has been largely used to investigate the etiopathological mechanisms of WBS, although pharmacological therapies have not been identified yet. Surprisingly, CD mice were so far mainly tested in adulthood, despite the developmental nature of WBS and the critical relevance of early timing for potential treatments. Here we provide for the first time a phenotypic characterization of CD mice of both sexes during infancy and adolescence, i.e., between birth and 7 weeks of age. CD pups of both sexes showed reduced body growth, delayed sensory development, and altered patterns of ultrasonic vocalizations and exploratory behaviors. Adolescent CD mice showed reduced locomotion and acoustic startle response, and altered social interaction and communication, the latter being more pronounced in female mice. Juvenile CD mutants of both sexes also displayed reduced brain weight, cortical and hippocampal dendritic length, and spine density. Our findings highlight the critical relevance of early neurobehavioral alterations as biomarkers of WBS pathology, underlying the importance of adolescence for identifying novel therapeutic targets for this neurological disorder.
威廉姆斯-比伦综合征(WBS)是一种由染色体微缺失(7q11.23)引起的神经发育障碍。WBS 已通过具有等效小鼠基因座完全缺失(CD)的小鼠系进行建模。该模型已被广泛用于研究 WBS 的病因发病机制,尽管尚未确定药理学治疗方法。令人惊讶的是,尽管 WBS 具有发育性质,并且早期时间对潜在治疗具有关键意义,但迄今为止,CD 小鼠主要在成年期进行测试。在这里,我们首次提供了两性 CD 小鼠在婴儿期和青春期(即出生到 7 周龄)期间的表型特征描述。两性 CD 幼鼠的体重增长减少,感觉发育延迟,并且超声发声和探索行为模式发生改变。青春期 CD 小鼠的运动和听觉惊跳反应减少,社交互动和交流改变,后者在雌性小鼠中更为明显。两性 CD 突变体幼鼠的大脑重量、皮质和海马树突长度以及棘突密度也减少。我们的研究结果强调了早期神经行为改变作为 WBS 病理生物标志物的关键意义,这凸显了青春期对于确定这种神经障碍的新治疗靶点的重要性。