Molecular evaluation and vector integration analysis of HCC complicating AAV gene therapy for hemophilia B.
作者信息
Schmidt Manfred, Foster Graham R, Coppens Michiel, Thomsen Hauke, Dolmetsch Ricardo, Heijink Liesbeth, Monahan Paul E, Pipe Steven W
机构信息
GeneWerk GmbH, Heidelberg, Germany.
Barts Liver Centre, Queen Mary University of London, London, United Kingdom.
出版信息
Blood Adv. 2023 Sep 12;7(17):4966-4969. doi: 10.1182/bloodadvances.2023009876.
Abstract
摘要
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Mol Ther Nucleic Acids. 2022 Aug 24;29:852-861. doi: 10.1016/j.omtn.2022.08.027. eCollection 2022 Sep 13.
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