From Failure to Meet the Clinical Endpoint to U.S. Food and Drug Administration Approval: 15th Antisense Oligonucleotide Therapy Approved Qalsody (Tofersen) for Treatment of Mutated Amyotrophic Lateral Sclerosis.
作者信息
van Roon-Mom Willeke, Ferguson Chantal, Aartsma-Rus Annemieke
机构信息
Department of Human Genetics, Dutch Center for RNA Therapeutics, Leiden University Medical Center, Leiden, The Netherlands.
Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
出版信息
Nucleic Acid Ther. 2023 Aug;33(4):234-237. doi: 10.1089/nat.2023.0027.
PMID:37581487
Abstract
摘要
Zotero 插件