Prospects and challenges of in vivo hematopoietic stem cell genome editing for hemoglobinopathies.
作者信息
Lieber André, Kiem Hans-Peter
机构信息
University of Washington, Seattle, WA, USA.
University of Washington, Seattle, WA, USA; Fred Hutchinson Cancer Center, Seattle, WA, USA.
出版信息
Mol Ther. 2023 Oct 4;31(10):2823-2825. doi: 10.1016/j.ymthe.2023.09.006. Epub 2023 Sep 19.
Abstract
摘要
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