Mayo Clinic College of Medicine and Science, Rochester, MN, USA.
Department of Hospital Medicine, Mayo Clinic, Jacksonville, FL, USA.
Am J Case Rep. 2023 Nov 14;24:e941789. doi: 10.12659/AJCR.941789.
BACKGROUND Immunotherapy is a novel treatment offering an alternative to traditional chemotherapeutic agents for different malignancies. Hematologic adverse reactions (HARs) related to immune checkpoint inhibitors (ICIs) are uncommon. Pure red cell aplasia (PRCA) is a rare hematologic complication of ICI therapy in metastatic melanoma with significant mortality risk despite treatment with steroids or immunosuppressive therapy. For unexplained acute anemia after exclusion of other causes, performing bone marrow biopsy is imperative to diagnose PRCA and rule out involvement of bone marrow by primary tumor. HARs can occur during ICI therapy or even after ICI therapy is stopped. ICI rechallenge, even after the development of HARs, is considered in some patients with good response to treatment of HARs from ICIs. Recurrence of HARs with the same or different type of reaction is seen in some patients. CASE REPORT Two cases of ICI-induced PRCA were confirmed on bone marrow biopsy after dual ICI treatment with nivolumab and ipilimumab in metastatic melanoma. In case 2, PRCA was successfully treated with steroids and later rechallenged with single-agent nivolumab, causing mild ICI-induced immune thrombocytopenia, which did not require treatment with steroids. CONCLUSIONS It is crucial to increase clinician awareness of the possibility of PRCA development not only during treatment with ICI but also after finishing treatment with ICI; there is high mortality associated with missing an opportunity to diagnose and treat PRCA on time with favorable results. ICI rechallenge can be considered in patients who showed response to immunotherapy, especially those with limited alternative therapeutic options.
免疫疗法是一种新型治疗方法,可为不同的恶性肿瘤提供传统化疗药物的替代方案。免疫检查点抑制剂(ICI)相关的血液学不良反应(HARs)并不常见。纯红细胞再生障碍性贫血(PRCA)是转移性黑色素瘤中 ICI 治疗的一种罕见血液学并发症,尽管采用类固醇或免疫抑制疗法治疗,但仍存在显著的死亡风险。对于排除其他原因后的不明原因急性贫血,进行骨髓活检对于诊断 PRCA 和排除骨髓原发性肿瘤受累至关重要。HARs 可在 ICI 治疗期间发生,甚至在 ICI 治疗停止后发生。对于一些对 HARs 的 ICI 治疗反应良好的患者,考虑重新使用 ICI 进行治疗。在一些患者中,会出现相同或不同类型反应的 HARs 复发。
两名转移性黑色素瘤患者接受纳武单抗和伊匹单抗双重 ICI 治疗后,经骨髓活检确诊为 ICI 诱导的 PRCA。在病例 2 中,PRCA 经类固醇治疗成功,随后重新使用单药纳武单抗治疗,导致轻度 ICI 诱导的免疫性血小板减少症,无需类固醇治疗。
不仅在接受 ICI 治疗期间,而且在完成 ICI 治疗后,提高临床医生对 PRCA 发展可能性的认识至关重要;如果未能及时诊断和治疗 PRCA,将会错失机会,导致高死亡率,而治疗结果良好。对于对免疫治疗有反应的患者,特别是那些治疗选择有限的患者,可以考虑重新使用 ICI。