Xia Lu, Nan Bin, Li Yi
Department of Biostatistics, University of Washington.
Department of Statistics, University of California, Irvine.
Ann Appl Stat. 2023 Dec;17(4):3550-3569. doi: 10.1214/23-aoas1775. Epub 2023 Oct 30.
The Scientific Registry of Transplant Recipients (SRTR) system has become a rich resource for understanding the complex mechanisms of graft failure after kidney transplant, a crucial step for allocating organs effectively and implementing appropriate care. As transplant centers that treated patients might strongly confound graft failures, Cox models stratified by centers can eliminate their confounding effects. Also, since recipient age is a proven non-modifiable risk factor, a common practice is to fit models separately by recipient age groups. The moderate sample sizes, relative to the number of covariates, in some age groups may lead to biased maximum stratified partial likelihood estimates and unreliable confidence intervals even when samples still outnumber covariates. To draw reliable inference on a comprehensive list of risk factors measured from both donors and recipients in SRTR, we propose a de-biased lasso approach via quadratic programming for fitting stratified Cox models. We establish asymptotic properties and verify via simulations that our method produces consistent estimates and confidence intervals with nominal coverage probabilities. Accounting for nearly 100 confounders in SRTR, the de-biased method detects that the graft failure hazard nonlinearly increases with donor's age among all recipient age groups, and that organs from older donors more adversely impact the younger recipients. Our method also delineates the associations between graft failure and many risk factors such as recipients' primary diagnoses (e.g. polycystic disease, glomerular disease, and diabetes) and donor-recipient mismatches for human leukocyte antigen loci across recipient age groups. These results may inform the refinement of donor-recipient matching criteria for stakeholders.
移植受者科学注册系统(SRTR)已成为了解肾移植后移植物失败复杂机制的丰富资源,这是有效分配器官和实施适当护理的关键一步。由于治疗患者的移植中心可能会严重混淆移植物失败情况,按中心分层的Cox模型可以消除其混杂效应。此外,由于受者年龄是一个已被证实的不可改变的风险因素,常见的做法是按受者年龄组分别拟合模型。相对于协变量数量而言,某些年龄组的样本量适中,即使样本数量仍超过协变量数量,也可能导致最大分层偏似然估计有偏差且置信区间不可靠。为了对从SRTR中测量的供体和受者的综合风险因素列表得出可靠推断,我们提出了一种通过二次规划的去偏套索方法来拟合分层Cox模型。我们建立了渐近性质,并通过模拟验证我们的方法产生具有标称覆盖概率的一致估计和置信区间。考虑到SRTR中近100个混杂因素,去偏方法检测到在所有受者年龄组中,移植物失败风险随供体年龄非线性增加,并且来自老年供体的器官对年轻受者的负面影响更大。我们的方法还描绘了移植物失败与许多风险因素之间的关联,例如受者的主要诊断(如多囊肾病、肾小球疾病和糖尿病)以及不同受者年龄组中人类白细胞抗原位点的供体 - 受者错配。这些结果可能为利益相关者完善供体 - 受者匹配标准提供参考。