School of Basic Medical Sciences, Institute of Cardiovascular Sciences, Peking University Health Science Center, Beijing, 100191, China.
Department of Cardiology, Boston Children's Hospital, Boston, MA, USA.
Acta Pharmacol Sin. 2024 Dec;45(12):2540-2552. doi: 10.1038/s41401-024-01348-y. Epub 2024 Jul 23.
Z-discs are core ultrastructural organizers of cardiomyocytes that modulate many facets of cardiac pathogenesis. Yet a comprehensive proteomic atlas of Z-disc-associated components remain incomplete. Here, we established an adeno-associated virus (AAV)-delivered, cardiomyocyte-specific, proximity-labeling approach to characterize the Z-disc proteome in vivo. We found palmdelphin (PALMD) as a novel Z-disc-associated protein in both adult murine cardiomyocytes and human pluripotent stem cell-derived cardiomyocytes. Germline and cardiomyocyte-specific Palmd knockout mice were grossly normal at baseline but exhibited compromised cardiac hypertrophy and aggravated cardiac injury upon long-term isoproterenol treatment. By contrast, cardiomyocyte-specific PALMD overexpression was sufficient to mitigate isoproterenol-induced cardiac injury. PALMD ablation perturbed the transverse tubule (T-tubule)-sarcoplasmic reticulum (SR) ultrastructures, which formed the Z-disc-associated junctional membrane complex (JMC) essential for calcium handling and cardiac function. These phenotypes were associated with the reduction of nexilin (NEXN), a crucial Z-disc-associated protein that is essential for both Z-disc and JMC structures and functions. PALMD interacted with NEXN and enhanced its protein stability while the Nexn mRNA level was not affected. AAV-based NEXN addback rescued the exacerbated cardiac injury in isoproterenol-treated PALMD-depleted mice. Together, this study discovered PALMD as a potential target for myocardial protection and highlighted in vivo proximity proteomics as a powerful approach to nominate novel players regulating cardiac pathogenesis.
Z 盘是心肌细胞的核心超微结构组织者,调节着心脏发病机制的许多方面。然而,Z 盘相关成分的综合蛋白质组图谱仍然不完整。在这里,我们建立了一种腺相关病毒 (AAV) 介导的、心肌细胞特异性的、接近标记方法,以在体内描述 Z 盘蛋白质组。我们发现棕榈醇结合蛋白 (PALMD) 是成年小鼠心肌细胞和人多能干细胞衍生的心肌细胞中一种新的 Z 盘相关蛋白。PALMD 基因敲除的种系和心肌细胞特异性小鼠在基线时大体上正常,但在长期异丙肾上腺素治疗后表现出心脏肥厚受损和心脏损伤加重。相比之下,心肌细胞特异性 PALMD 过表达足以减轻异丙肾上腺素引起的心脏损伤。PALMD 缺失破坏了形成钙处理和心脏功能所必需的 Z 盘相关连接膜复合物 (JMC) 的横管 (T 管)-肌浆网 (SR) 超微结构。这些表型与连接蛋白 (NEXN) 的减少有关,NEXN 是一种至关重要的 Z 盘相关蛋白,对 Z 盘和 JMC 的结构和功能都很重要。PALMD 与 NEXN 相互作用并增强其蛋白质稳定性,而 NEXN mRNA 水平不受影响。基于 AAV 的 NEXN 补体挽救了异丙肾上腺素处理的 PALMD 耗竭小鼠中加剧的心脏损伤。总之,这项研究发现 PALMD 是心肌保护的潜在靶点,并强调了体内接近蛋白质组学作为一种鉴定调节心脏发病机制的新分子的有力方法。