Laboratory of Pluripotent Stem Cell Disease Modeling, Translational Medicine Division, Research Branch, Sidra Medicine, P.O. Box 26999, Doha, Qatar.
College of Health and Life Sciences, Hamad Bin Khalifa University (HBKU), Qatar Foundation, Education City, Doha, Qatar.
Cell Mol Biol Lett. 2024 Sep 8;29(1):120. doi: 10.1186/s11658-024-00640-3.
Glucokinase (GCK), a key enzyme in glucose metabolism, plays a central role in glucose sensing and insulin secretion in pancreatic β-cells, as well as glycogen synthesis in the liver. Mutations in the GCK gene have been associated with various monogenic diabetes (MD) disorders, including permanent neonatal diabetes mellitus (PNDM) and maturity-onset diabetes of the young (MODY), highlighting its importance in maintaining glucose homeostasis. Additionally, GCK gain-of-function mutations lead to a rare congenital form of hyperinsulinism known as hyperinsulinemic hypoglycemia (HH), characterized by increased enzymatic activity and increased glucose sensitivity in pancreatic β-cells. This review offers a comprehensive exploration of the critical role played by the GCK gene in diabetes development, shedding light on its expression patterns, regulatory mechanisms, and diverse forms of associated monogenic disorders. Structural and mechanistic insights into GCK's involvement in glucose metabolism are discussed, emphasizing its significance in insulin secretion and glycogen synthesis. Animal models have provided valuable insights into the physiological consequences of GCK mutations, although challenges remain in accurately recapitulating human disease phenotypes. In addition, the potential of human pluripotent stem cell (hPSC) technology in overcoming current model limitations is discussed, offering a promising avenue for studying GCK-related diseases at the molecular level. Ultimately, a deeper understanding of GCK's multifaceted role in glucose metabolism and its dysregulation in disease states holds implications for developing targeted therapeutic interventions for diabetes and related disorders.
葡萄糖激酶(GCK)是葡萄糖代谢中的关键酶,在胰腺β细胞的葡萄糖感应和胰岛素分泌以及肝脏中的糖原合成中发挥核心作用。GCK 基因的突变与各种单基因糖尿病(MD)疾病有关,包括新生儿永久性糖尿病(PNDM)和青年发病的成年型糖尿病(MODY),突出了其在维持葡萄糖内稳态中的重要性。此外,GCK 获得性功能突变导致一种罕见的先天性高胰岛素血症,称为高胰岛素血症性低血糖(HH),其特征是胰腺β细胞中的酶活性增加和葡萄糖敏感性增加。本综述全面探讨了 GCK 基因在糖尿病发展中的关键作用,阐明了其表达模式、调控机制以及与单基因疾病的多种形式的关联。讨论了 GCK 参与葡萄糖代谢的结构和机制见解,强调了其在胰岛素分泌和糖原合成中的重要性。动物模型为 GCK 突变的生理后果提供了有价值的见解,尽管在准确再现人类疾病表型方面仍存在挑战。此外,还讨论了人类多能干细胞(hPSC)技术在克服当前模型限制方面的潜力,为在分子水平上研究 GCK 相关疾病提供了有前途的途径。最终,深入了解 GCK 在葡萄糖代谢中的多方面作用及其在疾病状态下的失调,对于开发针对糖尿病和相关疾病的靶向治疗干预具有重要意义。