Saha Shubhra Jyoti, Cheloha Ross W
Laboratory of Bioorganic Chemistry, National Institutes of Diabetes, Digestive and Kidney Diseases, National Institutes of Health, Bethesda, Maryland 20892, United States.
JACS Au. 2024 Nov 25;4(12):4780-4789. doi: 10.1021/jacsau.4c00711. eCollection 2024 Dec 23.
Methods that enable the on-demand synthesis of biologically active molecules offer the potential for a high degree of control over the timing and context of target activation; however, such approaches often require extensive engineering to implement. Tools to restrict the localization of assembly also remain limited. Here we present a new approach for stimulus-induced ligand assembly that helps to address these challenges. This methodology relies on the high affinity and specificity recognition exhibited by antibody fragments (nanobodies, Nbs). By using Nbs that recognize short peptide epitopes to create semisynthetic conjugates, we develop a bioengineering platform termed peptide epitope dimerization (PED) in which the addition of heterodimeric peptide composed of two Nb epitopes stimulates the proximity-induced synthesis of a functional ligand for the parathyroid hormone receptor-1, a G protein-coupled receptor. We further demonstrate that high efficiency assembly can be achieved on the cell surface via Nb-based delivery of template. This approach opens the door for the on-demand generation of bioactive receptor ligands preferentially at a desired biological niche.
能够按需合成生物活性分子的方法为高度控制靶点激活的时间和背景提供了潜力;然而,此类方法通常需要大量工程设计来实施。限制组装定位的工具也仍然有限。在此,我们提出一种刺激诱导配体组装的新方法,有助于应对这些挑战。该方法依赖于抗体片段(纳米抗体,Nbs)所表现出的高亲和力和特异性识别。通过使用识别短肽表位的纳米抗体来创建半合成缀合物,我们开发了一个称为肽表位二聚化(PED)的生物工程平台,其中添加由两个纳米抗体表位组成的异源二聚体肽可刺激甲状旁腺激素受体-1(一种G蛋白偶联受体)功能性配体的邻近诱导合成。我们进一步证明,通过基于纳米抗体的模板递送可在细胞表面实现高效组装。这种方法为在所需生物龛位优先按需生成生物活性受体配体打开了大门。