He Chuyu, Wang Xuejuan, Chiou Yi-Shiou, Basappa Basappa, Zhu Tao, Pandey Vijay, Lobie Peter E
Institute of Biopharmaceutical and Health Engineering and Tsinghua Berkeley Shenzhen Institute, Tsinghua Shenzhen International Graduate School, Tsinghua University, Shenzhen, PR China.
Master Degree Program in Toxicology, College of Pharmacy, Kaohsiung Medical University, Kaohsiung, Taiwan.
Cell Death Dis. 2025 Feb 7;16(1):76. doi: 10.1038/s41419-025-07387-5.
The interaction between HER2 and ERα signaling pathways contributes to resistance to anti-estrogen and HER2-targeted therapies, presenting substantial treatment challenges in ER-positive (ER+) HER2-positive (HER2+) mammary carcinoma (MC). Trefoil Factor-3 (TFF3) has been reported to mediate resistance to both anti-estrogen and anti-HER2 targeted therapies in ER+ and ER+HER2+ MC, respectively. Herein, the function and mechanism of TFF3 in ER+HER2+ MC were delineated; and novel combinatorial therapeutic strategies were identified. Elevated expression of TFF3 promoted the oncogenicity of ER+HER2+ MC cells, including enhanced cell proliferation, survival, anchorage-independent growth, 3D growth, cancer stem cell-like (CSC-like) phenotype, migration, invasion, and xenograft growth. Targeting TFF3 with an interfering RNA plasmid or a small-molecule inhibitor (AMPC) inhibited these oncogenic characteristics, highlighting the therapeutic potential of targeting TFF3 in ER+HER2+ MC. Furthermore, a high-throughput combinatorial anti-cancer compound library screening revealed that AMPC preferentially synergized with receptor tyrosine kinase c-MET inhibitors (c-METis) to reduce cell survival and the CSC-like phenotype. The combination of AMPC and c-METis also synergistically suppressed the in vivo growth of ER+HER2+ MC cell-derived xenografts and abrogated lung metastasis. Mechanistically, TFF3 was observed to activate c-MET signaling through a positive-feedback loop to enhance the CSC-like phenotype of ER+HER2+ MC. Therefore, proof of concept is provided herein that antagonizing of TFF3 is a promising therapeutic strategy in combination with c-MET inhibition for the treatment of ER+HER2+ MC.
HER2与雌激素受体α(ERα)信号通路之间的相互作用导致对抗雌激素和HER2靶向治疗产生耐药性,这给雌激素受体阳性(ER+)、人表皮生长因子受体2阳性(HER2+)的乳腺癌(MC)带来了巨大的治疗挑战。据报道,三叶因子3(TFF3)分别介导ER+和ER+HER2+ MC对抗雌激素和抗HER2靶向治疗的耐药性。在此,我们阐述了TFF3在ER+HER2+ MC中的功能和机制,并确定了新的联合治疗策略。TFF3表达升高促进了ER+HER2+ MC细胞的致癌性,包括增强细胞增殖、存活、非锚定依赖性生长、三维生长、癌症干细胞样(CSC样)表型、迁移、侵袭和异种移植生长。用干扰RNA质粒或小分子抑制剂(AMPC)靶向TFF3可抑制这些致癌特性,突出了靶向TFF3在ER+HER2+ MC中的治疗潜力。此外,高通量联合抗癌化合物库筛选显示,AMPC优先与受体酪氨酸激酶c-MET抑制剂(c-METis)协同作用,以降低细胞存活率和CSC样表型。AMPC与c-METis的联合使用还协同抑制了ER+HER2+ MC细胞衍生的异种移植瘤的体内生长,并消除了肺转移。从机制上讲,观察到TFF3通过正反馈回路激活c-MET信号,以增强ER+HER2+ MC的CSC样表型。因此,本文提供了概念验证,即拮抗TFF3与抑制c-MET联合使用是治疗ER+HER2+ MC的一种有前景的治疗策略。