Fang Teng, Liu Lanting, Sun Hao, Zhang Xiaoyu, Sun Xiyue, Yu Zhen, Gong Lixin, Xie Shiyi, Zhao Yonglong, Li Yan, Qiu Lugui, An Gang, He Bin, Hao Mu
State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin, 300020, China.
State Key Laboratory of Functions and Applications of Medicinal Plants, Engineering Research Center for the Development and Application of Ethnic Medicine and TCM (Ministry of Education), Guizhou Provincial Key Laboratory of Pharmaceutics, School of Pharmacy, Guizhou Medical University, Guiyang, 550004, China.
Biomark Res. 2025 Apr 7;13(1):57. doi: 10.1186/s40364-025-00773-3.
Maintaining protein homeostasis is vital for multiple myeloma (MM) cell survival. Indirubin- 3-monoxime (I3MO), a potential MM therapeutic, inhibits proteasome activity, while histone deacetylase 6 (HDAC6) regulates autophagy. We developed I3MV- 8b, an I3MO derivative, integrating an HDAC6 inhibitor moiety to enhance dual inhibition of proteasome and autophagy pathways.
The anti-MM effects of I3MV- 8b were tested in vitro and in vivo. To identify downstream targets, RNA-seq and dual-luciferase reporter assays were performed. Additionally, ChIP-seq and IP-MS techniques were employed to elucidate the underlying molecular mechanism.
I3MV- 8b significantly suppressed MM cell proliferation and induced apoptosis. Combined with proteasome inhibitors, I3MV- 8b enhanced cytotoxicity by concurrently inhibiting proteasome and autophagy pathways. It reduced TRIM28 transcription, correlating with lower expression of proteasome subunits and autophagy-related genes. ChIP-seq revealed that TRIM28 binds to proteasome gene promoters, and its knockdown decreased proteasome subunit expression and activity. TRIM28 knockdown also impaired autophagosome formation. IP-MS and Co-IP assays showed TRIM28 interacted with 14-3 - 3ζ, a negative regulator of autophagy, promoting its ubiquitination and degradation. This interaction reduced autophagy regulation, further sensitizing cells to treatment.
I3MV- 8b offers a novel dual inhibition strategy targeting proteasome and autophagy, presenting a promising therapeutic option for MM.
维持蛋白质稳态对多发性骨髓瘤(MM)细胞存活至关重要。靛玉红-3-单肟(I3MO)是一种潜在的MM治疗药物,可抑制蛋白酶体活性,而组蛋白去乙酰化酶6(HDAC6)调节自噬。我们开发了I3MV-8b,一种I3MO衍生物,整合了HDAC6抑制剂部分,以增强对蛋白酶体和自噬途径的双重抑制。
在体外和体内测试I3MV-8b的抗MM作用。为了确定下游靶点,进行了RNA测序和双荧光素酶报告基因检测。此外,采用染色质免疫沉淀测序(ChIP-seq)和免疫沉淀-质谱(IP-MS)技术来阐明潜在的分子机制。
I3MV-8b显著抑制MM细胞增殖并诱导凋亡。与蛋白酶体抑制剂联合使用时,I3MV-8b通过同时抑制蛋白酶体和自噬途径增强细胞毒性。它降低了TRIM28的转录,这与蛋白酶体亚基和自噬相关基因的较低表达相关。ChIP-seq显示TRIM28与蛋白酶体基因启动子结合,其敲低降低了蛋白酶体亚基的表达和活性。TRIM28敲低也损害了自噬体的形成。IP-MS和免疫共沉淀(Co-IP)检测表明TRIM28与自噬的负调节因子14-3-3ζ相互作用,促进其泛素化和降解。这种相互作用降低了自噬调节,进一步使细胞对治疗敏感。
I3MV-8b提供了一种针对蛋白酶体和自噬的新型双重抑制策略,为MM提供了一种有前景的治疗选择。