Lee Chaemi, Kim Seong Soon, Bae Myung Ae, Kim Seong Hwan
Therapeutics & Biotechnology Division, Korea Research Institute of Chemical Technology (KRICT), Daejeon, 34114, Korea.
Graduate School of New Drug Discovery and Development, Chungnam National University, Daejeon, Korea.
Neurochem Res. 2025 Apr 25;50(3):154. doi: 10.1007/s11064-025-04404-z.
Parkinson's disease (PD) is one of neurodegenerative diseases characterized by the progressive loss of dopaminergic neurons in the substantia nigra. The development of a neuroprotective therapy is crucial for mitigating features and progression of PD. Since autophagy induction has recently emerged as a promising neuroprotective strategy, this study aimed to identify autophagy-inducing compounds and evaluate their neuroprotective activity. Among 3,200 compounds consisting of FDA-approved drugs or are under active development, 547 compounds targeting neurological diseases were filtered in, and three compounds (sertraline, tiagabine and bicifadine) were finally identified to exhibit the autophagy-inducing activity and also demonstrated the autophagy-dependent neuroprotective action by inhibiting the mammalian target of rapamycin (mTOR) in 6-hydroxydopamine (6-OHDA)-induced neurotoxicity in PC12 cells. Furthermore, the analysis of neurochemical changes suggested that the ability of those compounds to restore the quantity of cellular neurotransmitters such as betaine, 5-hydroxyindoleacetic acid and kynurenine might be linked to their neuroprotective function. In conclusion, compounds like sertraline, tiagabine, and bicifadine that have the ability to induce autophagy and inhibit mTOR might be repurposed as PD treatment to protect the neuronal cells.
帕金森病(PD)是一种神经退行性疾病,其特征是黑质中多巴胺能神经元逐渐丧失。开发神经保护疗法对于减轻帕金森病的症状和进展至关重要。由于自噬诱导最近已成为一种有前景的神经保护策略,本研究旨在鉴定自噬诱导化合物并评估其神经保护活性。在由FDA批准的药物或正在积极研发的3200种化合物中,筛选出547种针对神经疾病的化合物,最终确定三种化合物(舍曲林、噻加宾和比西发定)具有自噬诱导活性,并通过抑制雷帕霉素靶蛋白(mTOR)在6-羟基多巴胺(6-OHDA)诱导的PC12细胞神经毒性中表现出自噬依赖性神经保护作用。此外,神经化学变化分析表明,这些化合物恢复细胞神经递质如甜菜碱、5-羟吲哚乙酸和犬尿氨酸数量的能力可能与其神经保护功能有关。总之,像舍曲林、噻加宾和比西发定这样具有诱导自噬和抑制mTOR能力的化合物可能被重新用于帕金森病的治疗以保护神经元细胞。