Liu Sam Chi-Hao, Chang Koping, Chen Meng-Ling, Kuo Ming-Che, Wang Teh-Cheng, Wu Ruey-Meei
Department of Neurology, National Taiwan University College of Medicine, No.1, Jen Ai Road section 1, Taipei City, Taiwan (R.O.C.).
Department of Neurology, National Taiwan University Hospital, No.7, Chung Shan South Road, Taipei City, Taiwan (R.O.C.).
Acta Neuropathol Commun. 2025 May 7;13(1):94. doi: 10.1186/s40478-025-02014-y.
Multiple system atrophy (MSA) is a neurodegenerative disorder characterized by parkinsonism, cerebellar dysfunction, and autonomic failure. Key pathological features of MSA include the formation of glial cytoplasmic inclusions (GCIs) in oligodendrocytes (OLs), myelin loss, and neuroinflammation. Although both inflammation and myelination are known to be critical in MSA, the roles of myelin proteins and their relationship with inflammation have often been overlooked. In this study, we injected AAV-Olig001 vectors carrying either human SNCA (AAV-hSNCA) or eGFP (AAV-eGFP) into the striatum of TgM83 transgenic mice, which express the A53T mutant form of human alpha-synuclein (αSyn), as well as into wild-type (WT) mice. We then assessed myelin protein expression and inflammatory responses. TgM83 mice injected with AAV-hSNCA exhibited demyelination, increased activation of microglia and astrocytes, and altered cytokine and chemokine profiles (including IL-1α, IL-10, IL-12(p40), CCL2, CCL3, CCL4, and CCL5), compared to both WT mice and TgM83 mice injected with AAV-eGFP. Interestingly, myelin basic protein (MBP) levels were significantly elevated around the injection site in TgM83 mice injected with AAV-hSNCA. Notably, we observed a positive correlation between MBP expression and inflammatory markers, as indicated by Iba1 and GFAP staining. These findings suggest that hSNCA overexpression is associated with increased MBP levels and enhanced inflammatory responses, implicating that MBP and myelination processes may play previously underappreciated roles in the pathogenesis of MSA.
多系统萎缩(MSA)是一种神经退行性疾病,其特征为帕金森综合征、小脑功能障碍和自主神经功能衰竭。MSA的关键病理特征包括少突胶质细胞(OLs)中胶质细胞胞质内含物(GCIs)的形成、髓鞘脱失和神经炎症。尽管炎症和髓鞘形成在MSA中都至关重要,但髓鞘蛋白的作用及其与炎症的关系常常被忽视。在本研究中,我们将携带人SNCA(AAV-hSNCA)或eGFP(AAV-eGFP)的AAV-Olig001载体注射到表达人α-突触核蛋白(αSyn)A53T突变形式的TgM83转基因小鼠的纹状体中,以及野生型(WT)小鼠的纹状体中。然后我们评估了髓鞘蛋白表达和炎症反应。与注射AAV-eGFP的WT小鼠和TgM83小鼠相比,注射AAV-hSNCA的TgM83小鼠表现出脱髓鞘、小胶质细胞和星形胶质细胞的激活增加,以及细胞因子和趋化因子谱的改变(包括IL-1α、IL-10、IL-12(p40)、CCL2、CCL3、CCL4和CCL5)。有趣的是,在注射AAV-hSNCA的TgM83小鼠中,注射部位周围的髓鞘碱性蛋白(MBP)水平显著升高。值得注意的是,我们观察到MBP表达与炎症标志物之间存在正相关,Iba1和GFAP染色表明了这一点。这些发现表明,hSNCA的过表达与MBP水平升高和炎症反应增强有关,这意味着MBP和髓鞘形成过程可能在MSA的发病机制中发挥了先前未被充分认识的作用。