Coppo Rosanna
Fondazione Ricerca Molinette, 10129 Turin, Italy.
J Clin Med. 2025 Jun 7;14(12):4045. doi: 10.3390/jcm14124045.
IgA nephropathy (IgAN) is an inflammatory glomerular disease caused by the production of galactose-deficient IgA1 (Gd-IgA1), which induces the formation of autoantibodies and IgA immune complexes (IgAICs) that are ultimately deposited in the mesangium. This event triggers mesangial cell proliferation, cytokine release and complement activation, and both glomerular and interstitial damage, eventually leading to kidney function decline. Persisting proteinuria is the most relevant marker of disease progression. Systemic corticosteroids (CSs), a powerful anti-inflammatory approach, have shown kidney protective effects in early trials involving patients with IgAN at risk of progression with persistent proteinuria. However, later studies raised concerns regarding severe adverse events associated with high doses of methylprednisolone and questioned the long-term benefits. As a result, the KDIGO 2021 guidelines recommended limiting CS therapy to selected patients who accepted the high risk of adverse events. The treatment landscape shifted when reduced doses of methylprednisolone, combined with Pneumocystis pneumonia prophylaxis, demonstrated similar kidney protection compared to full methylprednisolone doses with fewer adverse events. An innovative approach involves a targeted budesonide formulation acting on Peyer's patches, the main site of Gd-IgA1 production. This treatment showed benefits comparable to systemic CSs, with valuable limitations of adverse events. Several new drugs targeting key pathogenetic events of IgAN are under investigation, with promising results published in recent months. These new therapies target B cell activation (and subsequent Gd-IgA1 production), the complement cascade triggered by IgAIC deposition and the endothelin system, a key amplifier of kidney damage that contributes to the chronicity of IgAN.
IgA肾病(IgAN)是一种由缺乏半乳糖的IgA1(Gd-IgA1)产生所引起的炎症性肾小球疾病,Gd-IgA1会诱导自身抗体和IgA免疫复合物(IgAICs)的形成,这些复合物最终沉积于系膜。这一事件引发系膜细胞增殖、细胞因子释放和补体激活,以及肾小球和间质损伤,最终导致肾功能下降。持续性蛋白尿是疾病进展最相关的标志物。全身用糖皮质激素(CSs)是一种强效抗炎方法,在早期涉及有持续性蛋白尿进展风险的IgAN患者的试验中显示出肾脏保护作用。然而,后来的研究引发了对与高剂量甲泼尼龙相关的严重不良事件的担忧,并对其长期益处提出质疑。因此,KDIGO 2021指南建议将CS治疗限于接受不良事件高风险的特定患者。当与肺孢子菌肺炎预防措施联合使用的低剂量甲泼尼龙显示出与全剂量甲泼尼龙相似的肾脏保护作用且不良事件较少时,治疗格局发生了变化。一种创新方法涉及一种作用于派尔集合淋巴结(Gd-IgA1产生的主要部位)的靶向布地奈德制剂。这种治疗显示出与全身用CSs相当的益处,且不良事件有显著局限性。几种针对IgAN关键发病机制事件的新药正在研究中,最近几个月已发表了有前景的结果。这些新疗法靶向B细胞活化(以及随后的Gd-IgA1产生)、由IgAIC沉积触发的补体级联反应以及内皮素系统,内皮素系统是肾脏损伤的关键放大因子,它促成了IgAN的慢性化。