Ratip S, Skuse D, Porter J, Wonke B, Yardumian A, Modell B
Department of Haematology, University College London Medical School.
Arch Dis Child. 1995 May;72(5):408-12. doi: 10.1136/adc.72.5.408.
Twenty eight patients with thalassaemia intermedia and their parents were interviewed using specifically designed questionnaires to evaluate psychosocial burden. Hospital notes were analysed for clinical burden. A wide variation was found for both patients and parents, ranging from virtually unaffected to severely affected. Normal sexual function and setting up a family were mentioned by patients and parents as being particularly important for quality of life. Over half (58%) of the patients had problems with sexual maturation and functioning, and continuous monitoring of all patients with thalassaemia intermedia by a paediatric endocrinologist is therefore strongly indicated. Most parents said, in light of their experiences, that they would opt for prenatal diagnosis and termination of affected pregnancies even if a genotype predicting the mild form of disorder were discovered.
使用专门设计的问卷对28例中间型地中海贫血患者及其父母进行了访谈,以评估心理社会负担。分析医院记录以了解临床负担。结果发现,患者及其父母的情况差异很大,从几乎未受影响到严重受影响不等。患者和父母均表示,正常的性功能和组建家庭对生活质量尤为重要。超过一半(58%)的患者存在性成熟和性功能方面的问题,因此强烈建议由儿科内分泌学家对所有中间型地中海贫血患者进行持续监测。大多数父母表示,鉴于他们的经历,即使发现了预测病情为轻度的基因型,他们也会选择产前诊断并终止受影响的妊娠。