Rosenthal W, Antaramian A, Gilbert S, Birnbaumer M
Department of Cell Biology, Baylor College of Medicine, Houston, Texas 77030.
J Biol Chem. 1993 Jun 25;268(18):13030-3.
The coding region of the human vasopressin type 2 receptor gene bears mutations in the individuals affected with congenital nephrogenic diabetes insipidus, a disease characterized by the inability of the kidney to concentrate urine in response to vasopressin. Although it is assumed that the mutations result in loss of receptor function, proof of this hypothesis is lacking. We introduced one of these naturally occurring point mutations leading to a single amino acid change (Arg137-->His) into wild type cDNA. The mutant protein was expressed, and the functional properties of the receptor were examined. The mutant receptor exhibited an unaltered binding affinity for vasopressin compared to the wild type but failed to stimulate the Gs/adenylyl cyclase system. These data provide biochemical proof that the mutant receptor is the cause of the disease.
在患有先天性肾性尿崩症的个体中,人类血管加压素2型受体基因的编码区存在突变。先天性肾性尿崩症的特征是肾脏无法对血管加压素作出反应而浓缩尿液。尽管推测这些突变会导致受体功能丧失,但这一假设缺乏证据。我们将导致单个氨基酸改变(精氨酸137→组氨酸)的一种自然发生的点突变引入野生型cDNA中。表达了突变蛋白,并检测了受体的功能特性。与野生型相比,突变受体对血管加压素的结合亲和力未改变,但无法刺激Gs/腺苷酸环化酶系统。这些数据提供了生化证据,证明突变受体是该疾病的病因。