Zagalak Julian A, Menzi Mirjam, Schmich Fabian, Jahns Hartmut, Dogar Afzal M, Wullschleger Florian, Towbin Harry, Hall Jonathan
Institute of Pharmaceutical Sciences, Department of Chemistry and Applied Biosciences, ETH Zurich, CH-8093 Zurich, Switzerland.
Computational Biology Group (CBG), Department of Biosystems Science and Engineering, ETH Zurich, CH-4058 Basel, Switzerland.
RNA. 2015 Dec;21(12):2132-42. doi: 10.1261/rna.053637.115. Epub 2015 Oct 29.
Short interfering RNAs (siRNAs) are mediators of RNA interference (RNAi), a commonly used technique for selective down-regulation of target gene expression. Using an equimolar mixture of A, G, C, and U phosphoramidites during solid-phase synthesis, we introduced degenerate positions into RNA guide and passenger strands so that, when annealed, a large pool of distinct siRNA duplexes with randomized base pairs at defined sites was created. We assessed the randomization efficiency by deep sequencing one of the RNAs. All possible individual sequences were present in the pool with generally an excellent distribution of bases. Melting temperature analyses suggested that pools of randomized guide and passenger strands RNAs with up to eight degenerate positions annealed so that mismatched base-pairing was minimized. Transfections of randomized siRNAs (rnd-siRNAs) into cells led to inhibition of luciferase reporters by a miRNA-like mechanism when the seed regions of rnd-siRNA guide strands were devoid of degenerate positions. Furthermore, the mRNA levels of a select set of genes associated with siRNA off-target effects were measured and indicated that rnd-siRNAs with degenerate positions in the seed likely show typical non-sequence-specific effects, but not miRNA-like off-target effects. In the wake of recent reports showing the preponderance of miRNA-like off-target effects of siRNAs, our findings are of value for the design of a novel class of easily prepared and universally applicable negative siRNA controls.
短干扰RNA(siRNA)是RNA干扰(RNAi)的介导因子,RNAi是一种常用于选择性下调靶基因表达的技术。在固相合成过程中,我们使用A、G、C和U亚磷酰胺的等摩尔混合物,在RNA引导链和过客链中引入简并位点,以便退火后产生大量在特定位点具有随机碱基对的不同siRNA双链体。我们通过对其中一种RNA进行深度测序来评估随机化效率。池中存在所有可能的单个序列,碱基分布总体良好。熔解温度分析表明,具有多达八个简并位点的随机化引导链和过客链RNA池退火后,错配碱基配对最小化。当随机化siRNA(rnd-siRNA)引导链的种子区域没有简并位点时,将其转染到细胞中会通过类似miRNA的机制抑制荧光素酶报告基因。此外,还测量了一组与siRNA脱靶效应相关的特定基因的mRNA水平,结果表明种子区域具有简并位点的rnd-siRNA可能表现出典型的非序列特异性效应,但没有类似miRNA的脱靶效应。鉴于最近的报告显示siRNA存在大量类似miRNA的脱靶效应,我们的发现对于设计一类新型的易于制备且普遍适用的阴性siRNA对照具有重要价值。