Department of Ophthalmology, Ninth People's Hospital, Shanghai Jiao Tong University School of Medicine, 200011, Shanghai, P.R. China.
Shanghai Key Laboratory of Orbital Diseases and Ocular Oncology, 200011, Shanghai, P.R. China.
Cell Death Dis. 2018 May 1;9(5):444. doi: 10.1038/s41419-018-0473-5.
One of the primary obstacles in the application of retinal progenitor cells (RPCs) to the treatment of retinal degenerative diseases, such as age-related macular degeneration (AMD) and retinitis pigmentosa (RP), is their limited ability to proliferate and differentiate into specific retinal neurons. In this study, we revealed that repressor element-1-silencing transcription factor (REST), whose expression could be transcriptionally and post-transcriptionally mediated by retinoic acid (RA, one isomeride of a vitamin A derivative used as a differentiation-inducing agent in many disease treatments), plays a pivotal role in the regulation of proliferation and differentiation of RPCs. Our results show that direct knockdown of endogenous REST reduced RPC proliferation but accelerated RPC differentiation toward retinal neurons, which phenocopied the observed effects of RA on RPCs. Further studies disclosed that the expression level of REST could be downregulated by RA not only through upregulating microRNA (miR)-29a, which directly interacted with the 3'-untranslated region (3'-UTR) of the REST mRNA, but also through promoting REST proteasomal degradation. These results show us a novel functional protein, REST, which regulates RPC proliferation and differentiation, can be mediated by RA. Understanding the mechanisms of REST and RA in RPC fate determination enlightens a promising future for the application of REST and RA in the treatment of retinal degeneration diseases.
视网膜祖细胞(RPCs)在治疗视网膜退行性疾病(如年龄相关性黄斑变性(AMD)和色素性视网膜炎(RP))中的应用面临的主要障碍之一是其增殖和分化为特定视网膜神经元的能力有限。在这项研究中,我们揭示了阻遏元件-1-沉默转录因子(REST)在 RPC 增殖和分化的调控中起着关键作用,其表达可以通过视黄酸(RA,一种维生素 A 衍生物的异构体,用作许多疾病治疗中的诱导分化剂)进行转录和转录后调节。我们的结果表明,内源性 REST 的直接敲低减少了 RPC 的增殖,但加速了 RPC 向视网膜神经元的分化,这模拟了 RA 对 RPC 的观察到的影响。进一步的研究揭示,RA 不仅可以通过上调 miR-29a (它直接与 REST mRNA 的 3'-非翻译区(3'-UTR)相互作用),还可以通过促进 REST 蛋白体降解来下调 REST 的表达水平。这些结果向我们展示了一种新型的功能蛋白 REST,它可以通过 RA 调节 RPC 的增殖和分化。了解 REST 和 RA 在 RPC 命运决定中的机制为 REST 和 RA 在治疗视网膜退行性疾病中的应用提供了一个有前途的未来。