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Equitable Access to Gene Therapy: A Call to Action for the American Society of Gene and Cell Therapy.

作者信息

Cornetta Kenneth, Patel Kirtika, Wanjiku Christopher Mwaniki, Busakhala Naftali

机构信息

Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis, IN 46202, USA.

Department of Immunology, Moi University School of Medicine, Eldoret, Kenya.

出版信息

Mol Ther. 2018 Dec 5;26(12):2715-2716. doi: 10.1016/j.ymthe.2018.11.002. Epub 2018 Nov 16.

DOI:10.1016/j.ymthe.2018.11.002
PMID:30454956
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC6277505/
Abstract
摘要

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本文引用的文献

1
Core outcome set for gene therapy in haemophilia: Results of the coreHEM multistakeholder project.血友病基因治疗的核心结局集：多利益相关者项目核心 HEM 的结果。
Haemophilia. 2018 Jul;24(4):e167-e172. doi: 10.1111/hae.13504. Epub 2018 May 20.
2
The financial burden and distress of patients with cancer: Understanding and stepping-up action on the financial toxicity of cancer treatment.癌症患者的经济负担和困境：了解并加强对癌症治疗的财务毒性的行动。
CA Cancer J Clin. 2018 Mar;68(2):153-165. doi: 10.3322/caac.21443. Epub 2018 Jan 16.
3
The state of gene therapy research in Africa, its significance and implications for the future.非洲基因治疗研究的现状、其意义及对未来的影响。
Gene Ther. 2017 Sep;24(9):581-589. doi: 10.1038/gt.2017.57. Epub 2017 Jul 10.
4
Broadening Participation in the Sciences within and from Africa: Purpose, Challenges, and Prospects.在非及非洲内部扩大参与科学活动：目的、挑战与前景。
CBE Life Sci Educ. 2017 Summer;16(2). doi: 10.1187/cbe.15-12-0265.
5
Gene therapies development: slow progress and promising prospect.基因疗法的发展：进展缓慢但前景广阔。
J Mark Access Health Policy. 2017 Jan 3;5(1):1265293. doi: 10.1080/20016689.2017.1265293. eCollection 2017.
6
Global Health Equity: Cancer Care Outcome Disparities in High-, Middle-, and Low-Income Countries.全球健康公平性：高、中、低收入国家的癌症治疗结果差异
J Clin Oncol. 2016 Jan 1;34(1):6-13. doi: 10.1200/JCO.2015.62.2860. Epub 2015 Nov 17.
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Glybera's second act: the curtain rises on the high cost of therapy.Glybera的第二幕：高昂治疗费用的帷幕拉开了。
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