generated hematopoietic stem cells from genome edited induced pluripotent stem cells are functional in platelet-targeted gene therapy of murine hemophilia A.
作者信息
Wang Dawei, Zhang Guowei, Gu Junjie, Shao Xiaohu, Dai Yuting, Li Jianfeng, Pan Xiaohong, Yao Shuxian, Xu Aining, Jin Ying, Huang Jinyan, Shi Qizhen, Zhu Jiang, Xi Xiaodong, Chen Zhu, Chen Saijuan
机构信息
State Key Laboratory of Medical Genomics, Shanghai Institute of Hematology, Ruijin Hospital Affiliated to Shanghai Jiao Tong University School of Medicine, Shanghai, China.
National Research Center for Translational Medicine, Shanghai Jiao Tong University School of Medicine, Shanghai, China.
出版信息
Haematologica. 2020 Apr;105(4):e175-e179. doi: 10.3324/haematol.2019.219089. Epub 2019 Jul 11.
Abstract
摘要
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