Division of Pulmonary Medicine, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio.
Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio.
Pediatr Pulmonol. 2019 Dec;54(12):2035-2043. doi: 10.1002/ppul.24484. Epub 2019 Sep 1.
Duchenne muscular dystrophy (DMD) is an X-linked, progressive neuromuscular disorder that results in chronic respiratory insufficiency and subsequently failure requiring noninvasive ventilation (NIV). Adherence to NIV in neuromuscular disorders and related barriers are poorly described. The aim of the current study was to assess NIV adherence, adherence barriers, and identify psychosocial predictors of adherence in young boys with early DMD-related sleep disordered breathing and recommended nocturnal NIV. This cross-sectional study included 42 youth with DMD with prescribed nocturnal NIV, and their caregivers. Caregivers and youth completed questionnaires assessing adherence barriers, psychosocial symptoms (eg, anxiety and depressive symptoms), and stress. Medical information pertinent to cardiopulmonary health and neurologic status at both enrollment and initiation of NIV was reviewed. Adherence to NIV, defined as percent days used and days used ≥4 hours/day was 56.1 ± 38.7% and 46.2 ± 40.6%, respectively. Average duration of use on days worn was 5.61 ± 4.23 hours. NIV usage was correlated with the severity of obstructive sleep apnea but not cardiopulmonary variables. Mask discomfort was the most commonly reported adherence barrier followed by behavioral barriers (eg, refusing to use). Multiple regression analyses revealed that internalizing behaviors (eg, anxiety and depressive symptoms) and total adherence barriers significantly predicted NIV adherence. Adherence to NIV in DMD is poor and similar to other pediatric chronic diseases. Our data suggest interventions targeting adherence barriers and patient internalizing symptoms may improve adherence to NIV in DMD.
杜氏肌营养不良症(DMD)是一种 X 连锁的进行性神经肌肉疾病,导致慢性呼吸功能不全,随后需要进行无创通气(NIV)。神经肌肉疾病和相关障碍中的 NIV 依从性和相关障碍的描述很差。本研究的目的是评估患有早期 DMD 相关睡眠呼吸障碍和建议夜间使用 NIV 的年轻男孩的 NIV 依从性、依从性障碍,并确定依从性的心理社会预测因素。这项横断面研究包括 42 名接受夜间 NIV 治疗的 DMD 青少年及其照顾者。照顾者和青少年完成了评估依从性障碍、心理社会症状(例如,焦虑和抑郁症状)和压力的问卷。审查了与心肺健康和神经病学状态相关的医学信息,这些信息在登记和开始 NIV 时都有记录。将 NIV 依从性定义为使用的天数百分比和每天使用≥4 小时的天数百分比,分别为 56.1±38.7%和 46.2±40.6%。佩戴日的平均使用时间为 5.61±4.23 小时。NIV 的使用与阻塞性睡眠呼吸暂停的严重程度相关,但与心肺变量无关。面罩不适是最常报告的依从性障碍,其次是行为障碍(例如,拒绝使用)。多元回归分析显示,内化行为(例如,焦虑和抑郁症状)和总依从性障碍显著预测 NIV 依从性。DMD 中的 NIV 依从性很差,与其他儿科慢性疾病相似。我们的数据表明,针对依从性障碍和患者内化症状的干预措施可能会提高 DMD 患者对 NIV 的依从性。