Duque-Afonso Jesús, Ihorst Gabriele, Waterhouse Miguel, Zeiser Robert, Wäsch Ralph, Bertz Hartmut, Yücel Mehtap, Köhler Thomas, Müller-Quernheim Joachim, Marks Reinhard, Finke Jürgen
Department of Hematology/Oncology/Stem Cell Transplantation, Faculty of Medicine and Medical Center, University of Freiburg, Freiburg, Germany.
Clinical Trials Unit, Faculty of Medicine and Medical Center, University of Freiburg, Freiburg, Germany.
Bone Marrow Transplant. 2021 Jan;56(1):110-120. doi: 10.1038/s41409-020-0986-2. Epub 2020 Jun 26.
The age of patients undergoing allogeneic hematopoietic cell transplantation (allo-HCT) has increased during the last decades, mainly due to improved reduced-intensity/toxicity conditioning protocols. A reduced-intensity conditioning based on fludarabin, carmustin/BCNU and melphalan (FBM) has been previously developed at our institution. Since we observed detrimental effects in individual patients with compromised lung function, efforts have been made in order to replace BCNU by thiotepa (FTM) to reduce toxicity. In this study, we retrospectively analyzed the outcome, GvHD incidence, lung function and organ toxicity of patients with a median age of 62 years (range 21-79) transplanted for malignant disease (96.7%, 62.3% in intermediate/advanced disease stage) at our institution after conditioning with FBM (n = 136) or FTM (n = 105) between 2013 and 2017. Median follow-up was 868 days (range 0-2615). In multivariate analysis for overall survival, no difference was detected between both conditioning protocols in the presence of impaired lung function, age, lower performance, and liver disease previous allo-HCT. In the subgroup analysis, FTM was not inferior to FBM in patients with pulmonary disease prior allo-HCT, lymphoid malignancies, and higher comorbidity index. In conclusion, the reduced-intensity FBM and FTM conditioning protocols show adequate antineoplastic efficacy and are suitable for patients with impaired lung function.
在过去几十年中,接受异基因造血细胞移植(allo-HCT)的患者年龄有所增加,这主要归因于强度降低/毒性降低的预处理方案得到改进。我们机构此前已开发出一种基于氟达拉滨、卡莫司汀/BCNU和马法兰(FBM)的低强度预处理方案。由于我们观察到肺功能受损的个体患者出现了有害影响,因此已努力用噻替派(FTM)替代BCNU以降低毒性。在本研究中,我们回顾性分析了2013年至2017年间在我们机构接受FBM(n = 136)或FTM(n = 105)预处理后移植治疗恶性疾病(96.7%,中/晚期疾病阶段占62.3%)的年龄中位数为62岁(范围21 - 79岁)患者的结局、移植物抗宿主病(GvHD)发生率、肺功能和器官毒性。中位随访时间为868天(范围0 - 2615天)。在总生存的多因素分析中,在肺功能受损、年龄、较低体能状态和既往allo-HCT有肝病的情况下,两种预处理方案之间未检测到差异。在亚组分析中,对于既往allo-HCT有肺部疾病、淋巴系统恶性肿瘤和较高合并症指数的患者,FTM并不劣于FBM。总之,低强度FBM和FTM预处理方案显示出足够的抗肿瘤疗效,适用于肺功能受损的患者。